Gene therapy of myotubular myopathy

被引:0
|
作者
Bello, A. Buj [1 ]
机构
[1] Genethon, INSERM, UMR 951, Evry, France
关键词
D O I
暂无
中图分类号
Q5 [生物化学]; Q7 [分子生物学];
学科分类号
071010 ; 081704 ;
摘要
S03.2
引用
收藏
页码:12 / 12
页数:1
相关论文
共 50 条
  • [1] Gene therapy of myotubular myopathy
    Mavilio, F.
    HUMAN GENE THERAPY, 2013, 24 (12) : A15 - A15
  • [2] Gene replacement therapy for myotubular myopathy
    Bello, Ana Buj
    HUMAN GENE THERAPY, 2014, 25 (11) : A9 - A9
  • [3] Gene therapy for myotubular myopathy under test
    Klein, Friederike
    FORTSCHRITTE DER NEUROLOGIE PSYCHIATRIE, 2024, 92 (04) : 116 - 116
  • [4] Gene therapy in myotubular myopathy: promising progress and future directions
    Pierson, Christopher R.
    ANNALS OF TRANSLATIONAL MEDICINE, 2015, 3 (05)
  • [5] Gene therapy strategies for X-linked myotubular myopathy
    Pierson, Christopher R.
    EXPERT OPINION ON ORPHAN DRUGS, 2018, 6 (03): : 193 - 202
  • [6] Gene therapy for X-linked myotubular myopathy: the challenges
    Voermans, Nicol C.
    Ferreiro, Ana
    Aartsema-Rus, Annemieke
    Jungbluth, Heinz
    LANCET NEUROLOGY, 2023, 22 (12): : 1089 - 1091
  • [7] Gene therapy of myotubular myopathy: from preclinical studies to a clinical trial
    Bello, A. Buj
    HUMAN GENE THERAPY, 2018, 29 (12) : A11 - A12
  • [8] Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy
    Wilson, James M.
    Flotte, Terence R.
    HUMAN GENE THERAPY, 2020, 31 (13-14) : 695 - 696
  • [9] Moving Forward after Two Deaths in a Gene Therapy Trial of Myotubular Myopathy
    Wilson J.M.
    Flotte T.R.
    Genetic Engineering and Biotechnology News, 2020, 40 (08): : 14+16
  • [10] Tamoxifen therapy in a murine model of myotubular myopathy
    Nika Maani
    Nesrin Sabha
    Kamran Rezai
    Arun Ramani
    Linda Groom
    Nadine Eltayeb
    Faranak Mavandadnejad
    Andrea Pang
    Giulia Russo
    Michael Brudno
    Volker Haucke
    Robert T. Dirksen
    James J. Dowling
    Nature Communications, 9