Moving Forward after Two Deaths in a Gene Therapy Trial of Myotubular Myopathy

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作者
Wilson J.M. [1 ]
Flotte T.R. [2 ]
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[1] Gene Therapy Program, University of Pennsylvania, Perelman School of Medicine, Philadelphia, PA
[2] Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA
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D O I
10.1089/gen.40.08.05
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[No abstract available]
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