Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy

被引：149
|
作者：
Wilson, James M. [1 ]
Flotte, Terence R. [2 ]
机构：
[1] Univ Penn, Perelman Sch Med, Gene Therapy Program, Philadelphia, PA 19104 USA
[2] Univ Massachusetts, Horae Gene Therapy Ctr, Med Sch, Worcester, MA 01605 USA
来源：
HUMAN GENE THERAPY | 2020年 / 31卷 / 13-14期
关键词：
D O I：
10.1089/hum.2020.182
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：695 / 696
页数：2
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