Developing lentiviral vectors for gene therapy of Wiskott-Aldrich syndrome

被引:0
|
作者
Evans-Galea, MV
Wielgosz, MM
Strom, TS
Hanawa, H
Cunningham, JM
Nienhuis, AW
机构
[1] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
[2] Memphis VA Med Ctr, Memphis, TN USA
[3] Nippon Med Coll, Tokyo 113, Japan
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
3170
引用
收藏
页码:866A / 867A
页数:2
相关论文
共 50 条
  • [31] Successful functional correction of T cells from Wiskott-Aldrich syndrome patients with lentiviral vectors
    Dupré, L
    Marangoni, F
    Follenzi, A
    Trifari, S
    Martino, S
    Tsuchiya, S
    Bordignon, C
    Naldini, L
    Aiuti, A
    Roncarolo, MG
    MOLECULAR THERAPY, 2004, 9 : S346 - S346
  • [32] Hematopoietic Stem Cell Gene Therapy For Wiskott-Aldrich Syndrome
    Witzel, Maximilian G. W.
    Braun, Christian J.
    Boztug, Kaan
    Paruzynski, Anna
    Albert, Michael H.
    Schwarzer, Adrian
    Modlich, Ute
    Beier, Rita
    Goehring, Gudrun
    Naundorf, Sonja
    Kuehlcke, Klaus
    Rose, Martina
    Fraser, Christopher
    Mathias, Liesl
    Ferrari, Rudolf
    Abboud, Miguel R.
    Al-Herz, Waleed
    Kondratenko, Irina
    Marodi, Laszlo
    Schlegelberger, Brigitte
    Baum, Christopher
    Schmidt, Manfred
    von Kalle, Christof
    Klein, Christoph
    BLOOD, 2013, 122 (21)
  • [33] Hematopoietic stem cell gene therapy of Wiskott-Aldrich syndrome
    Boztug, Kaan
    Dewey, Ricardo A.
    Diez, Ines Avedillo
    Schmidt, Manfred
    Schwarzwaelder, Kerstin
    Diestelhorst, Jana
    Naundorf, Sonja
    Kuehlcke, Klaus
    Kondratenko, Irina
    Marodi, Laszlo
    von Kalle, Christoph
    Welte, Karl
    Klein, Christoph
    HUMAN GENE THERAPY, 2007, 18 (10) : 961 - 961
  • [34] Stem-Cell Gene Therapy for the Wiskott-Aldrich Syndrome
    Boztug, Kaan
    Schmidt, Manfred
    Schwarzer, Adrian
    Banerjee, Pinaki P.
    Diez, Ines Avedillo
    Dewey, Ricardo A.
    Boehm, Marie
    Nowrouzi, Ali
    Ball, Claudia R.
    Glimm, Hanno
    Naundorf, Sonja
    Kuehlcke, Klaus
    Blasczyk, Rainer
    Kondratenko, Irina
    Marodi, Laszlo
    Orange, Jordan S.
    von Kalle, Christof
    Klein, Christoph
    NEW ENGLAND JOURNAL OF MEDICINE, 2010, 363 (20): : 1918 - 1927
  • [35] Hematopoietic stem cell gene therapy for Wiskott-Aldrich Syndrome
    Boztug, Kaan
    Dewey, Ricardo A.
    Diez, Ines Avedillo
    Manfred, Schmidt
    Kerstin, Schwarzwaelder
    Jana, Diestelhorst
    Sonja, Naundorf
    Klaus, Kuehlke
    Irina, Kondratenko
    Laszlo, Marodi
    von Kalle, Christof
    Welte, Karl
    Klein, Christoph
    BLOOD, 2007, 110 (11) : 155A - 155A
  • [36] Gene therapy for Wiskott-Aldrich syndrome in a severely affected adult
    Morris, Emma C.
    Fox, Thomas
    Chakraverty, Ronjon
    Tendeiro, Rita
    Snell, Katie
    Rivat, Christine
    Grace, Sarah
    Gilmour, Kimberly
    Workman, Sarita
    Buckland, Karen
    Butler, Katie
    Chee, Ronnie
    Salama, Alan D.
    Ibrahim, Hazem
    Hara, Havinder
    Duret, Cecile
    Mavilio, Fulvio
    Male, Frances
    Bushman, Frederick D.
    Galy, Anne
    Burns, Siobhan O.
    Gaspar, H. Bobby
    Thrasher, Adrian J.
    BLOOD, 2017, 130 (11) : 1327 - 1335
  • [37] Natural gene therapy: Somatic reversion in the Wiskott-Aldrich syndrome
    Davis, Brian R.
    DiCola, Michael J.
    Prokopishyn, Nicole L.
    Rosenberg, Jonathan B.
    Moratto, Daniele
    Muul, Linda M.
    Candotti, Fabio
    Blaese, R. Michael
    BLOOD CELLS MOLECULES AND DISEASES, 2008, 40 (02) : 261 - 261
  • [38] Lentiviral-mediated gene therapy restores B cell tolerance in Wiskott-Aldrich syndrome patients
    Pala, Francesca
    Morbach, Henner
    Castle, Maria Carmina
    Schickel, Jean-Nicolas
    Scaramuzza, Samantha
    Chamberlain, Nicolas
    Cassani, Barbara
    Glauzy, Salome
    Romberg, Neil
    Candotti, Fabio
    Aiuti, Alessandro
    Bosticardo, Marita
    Villa, Anna
    Meffre, Eric
    JOURNAL OF CLINICAL INVESTIGATION, 2015, 125 (10): : 3941 - 3951
  • [39] WISKOTT-ALDRICH SYNDROME
    PRITIKIN, RI
    METABOLIC AND PEDIATRIC OPHTHALMOLOGY, 1980, 4 (02) : 106 - 106
  • [40] The Wiskott-Aldrich syndrome
    Orange, JS
    Stone, KD
    Turvey, SE
    Krzewski, K
    CELLULAR AND MOLECULAR LIFE SCIENCES, 2004, 61 (18) : 2361 - 2385