Improved Gene Therapy for Metachromatic Leukodystrophy

被引：0
|
作者：
Tricoli, Lucas [1 ]
Vanderver, Adeline [1 ]
Adang, Laura [1 ]
Chappell, Maxwell [1 ]
Breda, Laura [1 ]
Tanaka, Naoto [1 ]
Wenger, David [2 ]
Guerra, Amaliris [1 ]
Triebwasser, Michael [1 ]
Kurre, Peter [1 ]
Schlotawa, Lars [3 ]
Radhakrishnan, Karthikeyan [4 ]
Ahrens-Nicklas, Rebecca [1 ]
Hurwitz, Stephanie [5 ]
Rivella, Stefano [1 ]
机构：
[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[2] Thomas Jefferson Univ, Philadelphia, PA 19107 USA
[3] Univ Med Ctr Gottingen, Gottingen, Germany
[4] Bielefeld Univ, Bielefeld, Germany
[5] Hosp Univ Penn, Philadelphia, PA USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
876
引用
收藏
页码：415 / 416
页数：2
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