Improved Gene Therapy for Metachromatic Leukodystrophy

被引：0

作者：

Tricoli, Lucas ^{[1
]}

Vanderver, Adeline ^{[1
]}

Adang, Laura ^{[1
]}

Chappell, Maxwell ^{[1
]}

Breda, Laura ^{[1
]}

Tanaka, Naoto ^{[1
]}

Wenger, David ^{[2
]}

Guerra, Amaliris ^{[1
]}

Triebwasser, Michael ^{[1
]}

Kurre, Peter ^{[1
]}

Schlotawa, Lars ^{[3
]}

Radhakrishnan, Karthikeyan ^{[4
]}

Ahrens-Nicklas, Rebecca ^{[1
]}

Hurwitz, Stephanie ^{[5
]}

Rivella, Stefano ^{[1
]}

机构：

[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[2] Thomas Jefferson Univ, Philadelphia, PA 19107 USA

[3] Univ Med Ctr Gottingen, Gottingen, Germany

[4] Bielefeld Univ, Bielefeld, Germany

[5] Hosp Univ Penn, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2022年 / 30卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

876

引用

页码：415 / 416

页数：2

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