AAV9-CRiSPR/Cas9 preclinical trial on patient-derived FOXG1 mutated cells

被引：0

作者：

Croci, S. ^{[1
]}

Daga, S. ^{[1
]}

Lorenzetti, F. C. ^{[1
]}

Papa, F. T. ^{[1
]}

Donati, F. ^{[2
]}

Lo Rizzo, C. ^{[1
,3
]}

Lopergolo, D. ^{[1
,3
]}

Pancrazi, L. ^{[4
]}

Doria, M. ^{[5
]}

Auricchio, A. ^{[5
]}

Costa, M. ^{[4
]}

Conticello, S. ^{[2
]}

Renieri, A. ^{[1
,3
]}

Meloni, I. ^{[1
]}

机构：

[1] Univ Siena, Med Genet, Siena, Italy

[2] ITT Core Res Lab CRL, Mol Mech Oncogenesis, Florence, Italy

[3] Azienda Osped Univ Senese, Genet Med, Siena, Italy

[4] Italian Natl Res Council CNR, Lab Neurophysiol, Inst Neurosci, Pisa, Italy

[5] TIGEM Telethon Inst Genet & Med, Pozzuoli, Italy

来源：

EUROPEAN JOURNAL OF HUMAN GENETICS | 2019年 / 27卷

关键词：

D O I：

暂无

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

C20.5

引用

页码：853 / 853

页数：1

共 50 条

[41] Systemic Gene Editing for Muscular Dystrophy Using AAV-CRISPR/Cas9
Bengtsson, Niclas E.
Hall, John K.
Chamberlain, Jeffrey S.
MOLECULAR THERAPY, 2017, 25 (05) : 16 - 16
[42] One-step genetic correction of hemoglobin E/beta-thalassemia patient-derived iPSCs by the CRISPR/Cas9 system
Methichit Wattanapanitch
Nattaya Damkham
Ponthip Potirat
Kongtana Trakarnsanga
Montira Janan
Yaowalak U-pratya
Pakpoom Kheolamai
Nuttha Klincumhom
Surapol Issaragrisil
Stem Cell Research & Therapy, 9
[43] New Method of Genome Editing Derived From CRISPR/Cas9
Fang Rui
Chang Fei
Sun Zhao-Lin
Li Ning
Meng Qing-Yong
PROGRESS IN BIOCHEMISTRY AND BIOPHYSICS, 2013, 40 (08) : 691 - 702
[44] One-step genetic correction of hemoglobin E/beta-thalassemia patient-derived iPSCs by the CRISPR/Cas9 system
Wattanapanitch, Methichit
Damkham, Nattaya
Potirat, Ponthip
Trakarnsanga, Kongtana
Janan, Montira
U-pratya, Yaowalak
Kheolamai, Pakpoom
Klincumhom, Nuttha
Issaragrisil, Surapol
STEM CELL RESEARCH & THERAPY, 2018, 9
[45] Reversal of mitochondrial abnormalities by CRISPR/Cas9 editing of the mutant HTT allele in vitro in Huntington's Disease patient-derived pluripotent and neural stem cells
Lopes, Carla
Schlaeger, Thorsten
de Almeida, Luis Pereira
Daley, George
Rego, Cristina
EUROPEAN JOURNAL OF CLINICAL INVESTIGATION, 2019, 49 : 57 - 58
[46] CRISPR/Cas9: a tool to eradicate HIV-1
Ruchira Bhowmik
Binay Chaubey
AIDS Research and Therapy, 19
[47] CRISPR/Cas9: a tool to eradicate HIV-1
Bhowmik, Ruchira
Chaubey, Binay
AIDS RESEARCH AND THERAPY, 2022, 19 (01)
[48] CRISPR–Cas9 defence against HIV-1
Cláudio Nunes-Alves
Nature Reviews Microbiology, 2015, 13 (5) : 250 - 250
[49] CRISPR/Cas9 Mutagenesis by Translocation of Cas9 Protein Into Plant Cells via the Agrobacterium Type IV Secretion System
Schmitz, Daan J. J.
Ali, Zahir
Wang, Chenglong
Aljedaani, Fatimah
Hooykaas, Paul J. J.
Mahfouz, Magdy
de Pater, Sylvia
FRONTIERS IN GENOME EDITING, 2020, 2
[50] A review of CRISPR Cas9 for ASCVD: treatment strategies and could target PSCK9 gene using CRISPR cas9 prevent the patient from atherosclerotic vascular disease?
Suwito, Bambang Edi
Adji, Arga Setyo
Wardani, Vira Aulia Kusuma
Widjaja, Jordan Steven
Angel, Syalomitha Claudia Stefanie
Rahman, Firman Suryadi
BALI MEDICAL JOURNAL, 2022, 11 (02) : 985 - 993

← 1 2 3 4 5 →