AAV9-CRiSPR/Cas9 preclinical trial on patient-derived FOXG1 mutated cells

被引：0
|
作者：
Croci, S. [1 ]
Daga, S. [1 ]
Lorenzetti, F. C. [1 ]
Papa, F. T. [1 ]
Donati, F. [2 ]
Lo Rizzo, C. [1 ,3 ]
Lopergolo, D. [1 ,3 ]
Pancrazi, L. [4 ]
Doria, M. [5 ]
Auricchio, A. [5 ]
Costa, M. [4 ]
Conticello, S. [2 ]
Renieri, A. [1 ,3 ]
Meloni, I. [1 ]
机构：
[1] Univ Siena, Med Genet, Siena, Italy
[2] ITT Core Res Lab CRL, Mol Mech Oncogenesis, Florence, Italy
[3] Azienda Osped Univ Senese, Genet Med, Siena, Italy
[4] Italian Natl Res Council CNR, Lab Neurophysiol, Inst Neurosci, Pisa, Italy
[5] TIGEM Telethon Inst Genet & Med, Pozzuoli, Italy
来源：
EUROPEAN JOURNAL OF HUMAN GENETICS | 2019年 / 27卷
关键词：
D O I：
暂无
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
C20.5
引用
收藏
页码：853 / 853
页数：1
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