AAV9-CRiSPR/Cas9 preclinical trial on patient-derived FOXG1 mutated cells

被引：0

作者：

Croci, S. ^{[1
]}

Daga, S. ^{[1
]}

Lorenzetti, F. C. ^{[1
]}

Papa, F. T. ^{[1
]}

Donati, F. ^{[2
]}

Lo Rizzo, C. ^{[1
,3
]}

Lopergolo, D. ^{[1
,3
]}

Pancrazi, L. ^{[4
]}

Doria, M. ^{[5
]}

Auricchio, A. ^{[5
]}

Costa, M. ^{[4
]}

Conticello, S. ^{[2
]}

Renieri, A. ^{[1
,3
]}

Meloni, I. ^{[1
]}

机构：

[1] Univ Siena, Med Genet, Siena, Italy

[2] ITT Core Res Lab CRL, Mol Mech Oncogenesis, Florence, Italy

[3] Azienda Osped Univ Senese, Genet Med, Siena, Italy

[4] Italian Natl Res Council CNR, Lab Neurophysiol, Inst Neurosci, Pisa, Italy

[5] TIGEM Telethon Inst Genet & Med, Pozzuoli, Italy

来源：

EUROPEAN JOURNAL OF HUMAN GENETICS | 2019年 / 27卷

关键词：

D O I：

暂无

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

C20.5

引用

页码：853 / 853

页数：1

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