A Novel Gene Therapy Approach of Fanconi Anemia Hematopoietic Stem Cells Based on NHEJ-Mediated Gene Editing

被引：0
|
作者：
Roman-Rodriguez, Francisco J. [1 ,2 ]
Diez, Begona [1 ,2 ]
Alvarez, Lara [1 ,2 ]
Torres-Ruiz, Raul [3 ]
Corton, Marta [2 ]
Diaz de Heredia, Cristina [4 ]
Sevilla, Julian [5 ]
Ayuso, Carmen [2 ]
Bueren, Juan A. [1 ,2 ]
Rio, Paula [1 ,2 ]
机构：
[1] CIEMAT CIBERER, Div Hematopoiet Innovat Therapies, Madrid, Spain
[2] UAM, Adv Therapies Unit, IIS FJD, Madrid, Spain
[3] CNIO, Mol Cytogenet Grp, Human Canc Genet Program, Madrid, Spain
[4] Hosp Univ Vall dHebron, Barcelona, Spain
[5] Hosp Nino Jesus, Madrid, Spain
来源：
MOLECULAR THERAPY | 2017年 / 25卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
165
引用
收藏
页码：79 / 79
页数：1
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