Gene Therapy Approach for Severe Congenital Neutropenia by CRISPR/Cas9 Gene-Editing of Hematopoietic Stem Cells and iPSCs

被引：0

作者：

Skokowa, Julia ^{[1
]}

Ritter, Malte ^{[1
]}

Nasri, Masoud ^{[1
]}

Mir, Perihan ^{[1
]}

Dannenmann, Benjamin ^{[1
]}

Klimiankou, Maksim ^{[1
]}

Aghaallaei, Nargessadat ^{[1
]}

Secker, Benjamin ^{[1
]}

Haaf, Jeremy ^{[1
]}

Bravo, Natalia Alejandra Borbaran ^{[1
]}

Zeidler, Cornelia ^{[2
]}

Bajoghli, Baubak ^{[1
]}

Xu, Yun ^{[1
]}

Welte, Karl ^{[1
]}

机构：

[1] Univ Hosp Tuebingen, Clin Immunol, Hematol, Oncol, Tubingen, Germany

[2] MHH, Clin Immunol, Hematol, Oncol, Hannover, Germany

来源：

MOLECULAR THERAPY | 2020年 / 28卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

371

引用

页码：166 / 167

页数：2

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