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- [1] Phenotypic correction of hematopoietic stem and progenitor cells from Fanconi anemia group A knockout mice using non-viral gene therapy with Sleeping Beauty transposon vectorsHUMAN GENE THERAPY, 2022, 33 (23-24) : A65 - A65Botezatu, L.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyGuenechea Amurrio, G.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Valencia, Spain Paul Ehrlich Inst, Langen, GermanyLustig, J.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyTeschke, L.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyMiskey, C.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyLlorente-Arroyo, D.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Valencia, Spain Paul Ehrlich Inst, Langen, GermanyMeza, N.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Valencia, Spain Paul Ehrlich Inst, Langen, GermanyLozano, M. L.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Valencia, Spain Paul Ehrlich Inst, Langen, GermanyHolstein, M.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyGrueso, E.论文数: 0 引用数: 0 h-index: 0机构: Francisco Vitoria Univ, Madrid, Spain Paul Ehrlich Inst, Langen, GermanyBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Valencia, Spain Paul Ehrlich Inst, Langen, GermanyIvics, Z.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, Germany
- [2] Gene Therapy Restores the Transcriptional Program of Fanconi Anemia Hematopoietic Stem CellsMOLECULAR THERAPY, 2023, 31 (04) : 758 - 758Rio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainLasaga, Miren论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainVilas-Zornoza, Amaia论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainPlanell, Nuria论文数: 0 引用数: 0 h-index: 0机构: Univ Publ Navarra UPNA, Complejo Hosp Navarra CHN, Navarrabiomed, IdiSNA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainAinciburu-Fernandez, Marina论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainMouzo, Daniel论文数: 0 引用数: 0 h-index: 0机构: Univ Publ Navarra UPNA, Complejo Hosp Navarra CHN, Navarrabiomed, IdiSNA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainUllate-Agote, Asier论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainAlignani, Diego论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainZubicaray, Josune论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainSchwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharma, Cranbury, NJ USA Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainProsper, Felipe论文数: 0 引用数: 0 h-index: 0机构: Univ Navarra, Ctr Appl Med Res CIMA, Pamplona, Spain Univ Navarra, Ctr Appl Med Res, Pamplona, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainGomez-Cabrero, David论文数: 0 引用数: 0 h-index: 0机构: Univ Publ Navarra UPNA, Complejo Hosp Navarra CHN, Navarrabiomed, IdiSNA, Pamplona, Spain King Abdullah Univ Sci & Technol KAUST, Thuwal, Saudi Arabia Kings Coll London, Ctr Host Microbiome Interact, Fac Dent Oral & Craniofacial Sci, London, England Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambient & Tecnol CIEMAT, Madrid, Spain
- [3] Hematopoietic Stem Cell Collection for the Gene Therapy of Fanconi Anemia PatientsMOLECULAR THERAPY, 2021, 29 (04) : 342 - 342Navarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSanchez, Rebeca论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainZubicaray, Josune论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGalvez, Eva论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainMerino, Eva论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSebastian, Elena论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAzqueta, Carmen论文数: 0 引用数: 0 h-index: 0机构: Banc Sang & Teixits Catalunya, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCasado, Jose A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlberquilla, Omaira论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBogliolo, Massimo论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Santa Creu & Sant Pau, IIB St Pau, Barcelona, Spain Univ Autonoma Barcelona, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRoman-Rodriguez, Francisco J.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGimenez, Yari论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLarcher, Lise论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Inst Rech St Louis, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSalgado, Rocio论文数: 0 引用数: 0 h-index: 0机构: Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainPujol, Roser M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Santa Creu & Sant Pau, IIB St Pau, Serv Genet, Barcelona, Spain Hosp Santa Creu & Sant Pau, IIB St Pau, Inst Reserca, Barcelona, Spain Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainHaldun, Raquel论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall dHebron, Vall dHebron Inst Recerca, Serv Oncol & Hematol Pediat, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCastillo, Ana论文数: 0 引用数: 0 h-index: 0机构: Anal Clin Hosp Infantil Univ Nino Jesus, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSoulier, Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, Inst Rech St Louis, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainQuerol, Sergi论文数: 0 引用数: 0 h-index: 0机构: Banc Sang & Teixits Catalunya, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainFernandez, Jesus论文数: 0 引用数: 0 h-index: 0机构: Banc Sang & Teixits Catalunya, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainShcwartz, Jonathan论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharmaceut Inc, New York, NY USA Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGarcia de Andoin, Nagore论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Donostia, San Sebastian, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLopez, Ricardo论文数: 0 引用数: 0 h-index: 0机构: Hosp Cruces, Bilbao, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCatala, Albert论文数: 0 引用数: 0 h-index: 0机构: Hosp St Joan de Deu, Dept Hematol Oncol, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSurralles, Jordi论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Hosp Santa Creu & Sant Pau, IIB St Pau, Serv Genet, Barcelona, Spain Hosp Santa Creu & Sant Pau, IIB St Pau, Inst Reserca, Barcelona, Spain Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainDiaz de Heredia, Cristina论文数: 0 引用数: 0 h-index: 0机构: Vall dHebron Inst Recerca, Serv Oncol & Hematol Pediat, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras CIBERER, Madrid, Spain Inst Invest Sanitarias Fdn Jimenez Diaz IIS FJD, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain
- [4] Efficient non-viral gene delivery by minicircle Sleeping Beauty transposon system into hematopoietic stem cells for gene therapy applicationsHUMAN GENE THERAPY, 2015, 26 (10) : A18 - A18Holstein, M.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyMesa-Nunez, C.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER IIS FJD, Div Hematopoiet Innovat Therapies, Madrid 28040, Spain Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyAlmarza, E.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER IIS FJD, Div Hematopoiet Innovat Therapies, Madrid 28040, Spain Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyMiskey, C.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanySchmeer, M.论文数: 0 引用数: 0 h-index: 0机构: PlasmidFactory GmbH & Co KG, D-33607 Bielefeld, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyKobelt, D.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Translat Oncol Solid Tumors, D-13125 Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyWalther, W.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Translat Oncol Solid Tumors, D-13125 Berlin, Germany Charite, Expt & Clin Res Ctr, Translat Oncol Solid Tumors, D-13125 Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyIzsvak, Z.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Mobile DNA, D-13125 Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanySchleef, M.论文数: 0 引用数: 0 h-index: 0机构: PlasmidFactory GmbH & Co KG, D-33607 Bielefeld, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyRudolph, C.论文数: 0 引用数: 0 h-index: 0机构: Univ Munich, Dept Pediat, D-80337 Munich, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER IIS FJD, Div Hematopoiet Innovat Therapies, Madrid 28040, Spain Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyGuenechea, G.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER IIS FJD, Div Hematopoiet Innovat Therapies, Madrid 28040, Spain Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, GermanyIvics, Z.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, Germany Paul Ehrlich Inst, Div Med Biotechnol, Transposit & Genome Engn, D-63225 Langen, Germany
- [5] Efficient non-viral gene delivery by minicircle Sleeping Beauty transposon system into hematopoietic stem cells for gene therapy applicationsHUMAN GENE THERAPY, 2014, 25 (11) : A76 - A76Swierczek, M.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanySchmeer, M.论文数: 0 引用数: 0 h-index: 0机构: PlasmidFactory GmbH & Co KG, D-33607 Bielefeld, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanySchleef, M.论文数: 0 引用数: 0 h-index: 0机构: PlasmidFactory GmbH & Co KG, D-33607 Bielefeld, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanyKobelt, D.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, D-13125 Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanyWalther, W.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, D-13125 Berlin, Germany Charite, Translat Oncol Expt & Clin Res Ctr, D-13125 Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanyIzsvak, Z.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Mobile DNA, Berlin, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, GermanyIvics, Z.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, Germany Paul Ehrlich Inst, Div Med Biotechnol, D-63225 Langen, Germany
- [6] Using Sleeping Beauty transposons as a non-viral approach for the correction of Fanconi Anemia cellsHUMAN GENE THERAPY, 2013, 24 (12) : A62 - A62Grueso, E.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, GermanyRio, P.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Madrid, Spain Paul Ehrlich Inst, Langen, GermanyIzsvak, Z.论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Berlin, Germany Paul Ehrlich Inst, Langen, GermanyBueren, J. A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Madrid, Spain Paul Ehrlich Inst, Langen, GermanyIvics, Z.论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Langen, Germany Paul Ehrlich Inst, Langen, Germany
- [7] Non-viral approach using Sleeping Beauty transposons for the correction of Fanconi Anemia CellsHUMAN GENE THERAPY, 2012, 23 (10) : A140 - A140Grueso, Esther论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, Germany Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, GermanyRio, Paula论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Hematopoiesis & Gene Therapy Div, Madrid, Spain Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, GermanyIzsvak, Zsuzsanna论文数: 0 引用数: 0 h-index: 0机构: Max Delbruck Ctr Mol Med, Mobile DNA Grp, Berlin, Germany Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, GermanyBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: CIEMAT CIBERER, Hematopoiesis & Gene Therapy Div, Madrid, Spain Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, GermanyIvics, Zoltan论文数: 0 引用数: 0 h-index: 0机构: Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, Germany Paul Ehrlich Inst, Transposit & Genome Engn Grp, D-6070 Langen, Germany
- [8] A Non-Viral Vector for Targeting Gene Therapy to Motoneurons in the CNSNEURODEGENERATIVE DISEASES, 2004, 1 (2-3) : 101 - 108Miana-Mena, Francisco J.论文数: 0 引用数: 0 h-index: 0机构: Lab Genet Bioquim, ES-50013 Zaragoza, Spain Fac Vet Zaragoza, Grp Sanguineos, ES-50013 Zaragoza, Spain Lab Genet Bioquim, ES-50013 Zaragoza, SpainMunoz, Maria J.论文数: 0 引用数: 0 h-index: 0机构: Fac Vet Zaragoza, Dept Farmacol & Fisiol, Zaragoza, Spain Lab Genet Bioquim, ES-50013 Zaragoza, SpainRoux, Sylvie论文数: 0 引用数: 0 h-index: 0机构: Inst Pasteur, Unite Embryol Mol, Paris, France Lab Genet Bioquim, ES-50013 Zaragoza, SpainCiriza, Jesus论文数: 0 引用数: 0 h-index: 0机构: Lab Genet Bioquim, ES-50013 Zaragoza, Spain Fac Vet Zaragoza, Grp Sanguineos, ES-50013 Zaragoza, Spain Lab Genet Bioquim, ES-50013 Zaragoza, SpainZaragoza, Pilar论文数: 0 引用数: 0 h-index: 0机构: Lab Genet Bioquim, ES-50013 Zaragoza, Spain Fac Vet Zaragoza, Grp Sanguineos, ES-50013 Zaragoza, Spain Lab Genet Bioquim, ES-50013 Zaragoza, Spain论文数: 引用数: h-index:机构:Osta, Rosario论文数: 0 引用数: 0 h-index: 0机构: Lab Genet Bioquim, ES-50013 Zaragoza, Spain Fac Vet Zaragoza, Grp Sanguineos, ES-50013 Zaragoza, Spain Lab Genet Bioquim, ES-50013 Zaragoza, Spain
- [9] Cyclophosphamide mediated selection of hematopoietic stem cells corrected by gene therapy in a model of Fanconi Anemia.AMERICAN JOURNAL OF HUMAN GENETICS, 1999, 65 (04) : A502 - A502Noll, M论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USABateman, RL论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USAD'Andrea, A论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USAGrompe, M论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USA
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