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- [21] Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaNature Medicine, 2019, 25 : 1396 - 1401Paula Río论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionSusana Navarro论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionWei Wang论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRebeca Sánchez-Domínguez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRoser M. Pujol论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJosé C. Segovia论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionMassimo Bogliolo论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionEva Merino论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionNing Wu论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRocío Salgado论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionMaría L. Lamana论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRosa M. Yañez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJosé A. Casado论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionYari Giménez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionFrancisco J. Román-Rodríguez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionLara Álvarez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionOmaira Alberquilla论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionAnna Raimbault论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionGuillermo Guenechea论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionM. Luz Lozano论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionLaura Cerrato论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionMiriam Hernando论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionEva Gálvez论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRaquel Hladun论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionIrina Giralt论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJordi Barquinero论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionAnne Galy论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionNagore García de Andoín论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionRicardo López论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionAlbert Catalá论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJonathan D. Schwartz论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJordi Surrallés论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJean Soulier论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionManfred Schmidt论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionCristina Díaz de Heredia论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJulián Sevilla论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies DivisionJuan A. Bueren论文数: 0 引用数: 0 h-index: 0机构: Centro de investigaciones Energéticas,Hematopoietic Innovative Therapies Division
- [22] Gene therapy: efficient targeting of hematopoietic stem cellsBLOOD, 2005, 106 (10) : 3333 - 3333论文数: 引用数: h-index:机构:
- [23] Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaNATURE MEDICINE, 2019, 25 (09) : 1396 - +Rio, Paula论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainNavarro, Susana论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainWang, Wei论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Div Translat Oncol, Heidelberg, Germany Natl Ctr Tumor Dis, Heidelberg, Germany GeneWerk, Heidelberg, Germany Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSanchez-Dominguez, Rebeca论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainPujol, Roser M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona, Spain Hosp Santa Creu & Sant Pau, Serv Genet, Barcelona, Spain Hosp Santa Creu & Sant Pau, Inst Invest Biomed, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSegovia, Jose C.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBogliolo, Massimo论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona, Spain Hosp Santa Creu & Sant Pau, Serv Genet, Barcelona, Spain Hosp Santa Creu & Sant Pau, Inst Invest Biomed, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainMerino, Eva论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed, Serv Hematol & Oncol Pediat, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainWu, Ning论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Div Translat Oncol, Heidelberg, Germany Natl Ctr Tumor Dis, Heidelberg, Germany Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSalgado, Rocio论文数: 0 引用数: 0 h-index: 0机构: Fdn Jimenez Diaz, Inst Invest Sanitarias, Hosp Univ Fdn Jimenez Diaz, Serv Hematol, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLamana, Maria L.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainYanez, Rosa M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCasado, Jose A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGimenez, Yari论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRoman-Rodriguez, Francisco J.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlvarez, Lara论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainAlberquilla, Omaira论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainRaimbault, Anna论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, IRSL, INSERM, CNRS, Paris, France Hop St Louis, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGuenechea, Guillermo论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLuz Lozano, M.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCerrato, Laura论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainHernando, Miriam论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGalvez, Eva论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed, Serv Hematol & Oncol Pediat, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainHladun, Raquel论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall dHebron, Serv Oncol & Hematol Pediat, Barcelona, Spain Vall dHebron Inst Recerca, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGiralt, Irina论文数: 0 引用数: 0 h-index: 0机构: Vall dHebron Inst Recerca, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBarquinero, Jordi论文数: 0 引用数: 0 h-index: 0机构: Vall dHebron Inst Recerca, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGaly, Anne论文数: 0 引用数: 0 h-index: 0机构: Genethon, Evry, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainGarcia de Andoin, Nagore论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Donostia, San Sebastian, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainLopez, Ricardo论文数: 0 引用数: 0 h-index: 0机构: Cruces Univ Hosp, Pediat Oncol & Hematol Unit, Osakidetza Basque Hlth Serv, Baracaldo, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainCatala, Albert论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp San Juan Dios, Serv Hematol & Oncol, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSchwartz, Jonathan D.论文数: 0 引用数: 0 h-index: 0机构: Rocket Pharma, New York, NY USA Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSurralles, Jordi论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Univ Autonoma Barcelona, Dept Genet & Microbiol, Barcelona, Spain Hosp Santa Creu & Sant Pau, Serv Genet, Barcelona, Spain Hosp Santa Creu & Sant Pau, Inst Invest Biomed, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSoulier, Jean论文数: 0 引用数: 0 h-index: 0机构: Univ Paris, IRSL, INSERM, CNRS, Paris, France Hop St Louis, Paris, France Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: German Canc Res Ctr, Div Translat Oncol, Heidelberg, Germany Natl Ctr Tumor Dis, Heidelberg, Germany GeneWerk, Heidelberg, Germany Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainDiaz de Heredia, Cristina论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall dHebron, Serv Oncol & Hematol Pediat, Barcelona, Spain Vall dHebron Inst Recerca, Barcelona, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainSevilla, Julian论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Hosp Infantil Univ Nino Jesus, Fdn Invest Biomed, Serv Hematol & Oncol Pediat, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, SpainBueren, Juan A.论文数: 0 引用数: 0 h-index: 0机构: Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain Ctr Invest Biomed Red Enfermedades Raras, Madrid, Spain Fdn Jimenez Diaz, Inst Invest Sanitarias, Madrid, Spain Ctr Invest Energet Medioambientales & Tecnol, Hematopoiet Innovat Therapies Div, Madrid, Spain
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