Cyclophosphamide mediated selection of hematopoietic stem cells corrected by gene therapy in a model of Fanconi Anemia.

被引：0
|
作者：
Noll, M
Bateman, RL
D'Andrea, A
Grompe, M
机构：
[1] Oregon Hlth Sci Univ, Dept Mol & Med Genet, Portland, OR 97201 USA
[2] Harvard Univ, Sch Med, Dana Farber Canc Inst, Dept Pediat Oncol, Boston, MA USA
来源：
AMERICAN JOURNAL OF HUMAN GENETICS | 1999年 / 65卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q3 [遗传学];
学科分类号：
071007 ; 090102 ;
摘要：
2860
引用
收藏
页码：A502 / A502
页数：1
相关论文
共 50 条
  • [1] Preclinical protocol for in vivo selection of hematopoietic stem cells corrected by gene therapy in Fanconi anemia group C
    Noll, M
    Bateman, RL
    D'Andrea, AD
    Grompe, M
    MOLECULAR THERAPY, 2001, 3 (01) : 14 - 23
  • [2] Improved Hematopoietic Gene Therapy in a Mouse Model of Fanconi Anemia Mediated by Mesenchymal Stromal Cells
    Fernandez-Garcia, Maria
    Luisa Lamana, Maria
    Hernando-Rodriguez, Miriam
    Sanchez-Dominguez, Rebeca
    Bueren, Juan
    Yanez, Rosa
    HUMAN GENE THERAPY, 2018, 29 (03) : 327 - 336
  • [3] Gene Therapy Restores the Transcriptional Program of Fanconi Anemia Hematopoietic Stem Cells
    Rio, Paula
    Lasaga, Miren
    Vilas-Zornoza, Amaia
    Planell, Nuria
    Navarro, Susana
    Ainciburu-Fernandez, Marina
    Mouzo, Daniel
    Ullate-Agote, Asier
    Alignani, Diego
    Zubicaray, Josune
    Schwartz, Jonathan
    Sevilla, Julian
    Prosper, Felipe
    Gomez-Cabrero, David
    Bueren, Juan A.
    MOLECULAR THERAPY, 2023, 31 (04) : 758 - 758
  • [4] A Novel Gene Therapy Approach of Fanconi Anemia Hematopoietic Stem Cells Based on NHEJ-Mediated Gene Editing
    Roman-Rodriguez, Francisco J.
    Diez, Begona
    Alvarez, Lara
    Torres-Ruiz, Raul
    Corton, Marta
    Diaz de Heredia, Cristina
    Sevilla, Julian
    Ayuso, Carmen
    Bueren, Juan A.
    Rio, Paula
    MOLECULAR THERAPY, 2017, 25 (05) : 79 - 79
  • [5] High incidence of hematopoietic stem cell mosaicism in fanconi anemia.
    Tolar, Jakub
    MacMillan, Margaret L.
    Batish, Sat Dev
    Eide, Cindy
    Flit, Yeva
    Davies, Stella M.
    Blazar, Bruce R.
    Auerbach, Arleen D.
    Wagner, John E.
    BLOOD, 2006, 108 (11) : 296A - 296A
  • [6] Hematopoietic Stem Cell Collection for the Gene Therapy of Fanconi Anemia Patients
    Navarro, Susana
    Sevilla, Julian
    Rio, Paula
    Sanchez, Rebeca
    Zubicaray, Josune
    Galvez, Eva
    Merino, Eva
    Sebastian, Elena
    Azqueta, Carmen
    Casado, Jose A.
    Segovia, Jose C.
    Alberquilla, Omaira
    Bogliolo, Massimo
    Roman-Rodriguez, Francisco J.
    Gimenez, Yari
    Larcher, Lise
    Salgado, Rocio
    Pujol, Roser M.
    Haldun, Raquel
    Castillo, Ana
    Soulier, Jean
    Querol, Sergi
    Fernandez, Jesus
    Shcwartz, Jonathan
    Garcia de Andoin, Nagore
    Lopez, Ricardo
    Catala, Albert
    Surralles, Jordi
    Diaz de Heredia, Cristina
    Bueren, Juan A.
    MOLECULAR THERAPY, 2021, 29 (04) : 342 - 342
  • [7] Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
    Rio, Paula
    Navarro, Susana
    Wang, Wei
    Sanchez-Dominguez, Rebeca
    Pujol, Roser M.
    Segovia, Jose C.
    Bogliolo, Massimo
    Merino, Eva
    Wu, Ning
    Salgado, Rocio
    Lamana, Maria L.
    Yanez, Rosa M.
    Casado, Jose A.
    Gimenez, Yari
    Roman-Rodriguez, Francisco J.
    Alvarez, Lara
    Alberquilla, Omaira
    Raimbault, Anna
    Guenechea, Guillermo
    Luz Lozano, M.
    Cerrato, Laura
    Hernando, Miriam
    Galvez, Eva
    Hladun, Raquel
    Giralt, Irina
    Barquinero, Jordi
    Galy, Anne
    Garcia de Andoin, Nagore
    Lopez, Ricardo
    Catala, Albert
    Schwartz, Jonathan D.
    Surralles, Jordi
    Soulier, Jean
    Schmidt, Manfred
    Diaz de Heredia, Cristina
    Sevilla, Julian
    Bueren, Juan A.
    NATURE MEDICINE, 2019, 25 (09) : 1396 - +
  • [8] Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
    Paula Río
    Susana Navarro
    Wei Wang
    Rebeca Sánchez-Domínguez
    Roser M. Pujol
    José C. Segovia
    Massimo Bogliolo
    Eva Merino
    Ning Wu
    Rocío Salgado
    María L. Lamana
    Rosa M. Yañez
    José A. Casado
    Yari Giménez
    Francisco J. Román-Rodríguez
    Lara Álvarez
    Omaira Alberquilla
    Anna Raimbault
    Guillermo Guenechea
    M. Luz Lozano
    Laura Cerrato
    Miriam Hernando
    Eva Gálvez
    Raquel Hladun
    Irina Giralt
    Jordi Barquinero
    Anne Galy
    Nagore García de Andoín
    Ricardo López
    Albert Catalá
    Jonathan D. Schwartz
    Jordi Surrallés
    Jean Soulier
    Manfred Schmidt
    Cristina Díaz de Heredia
    Julián Sevilla
    Juan A. Bueren
    Nature Medicine, 2019, 25 : 1396 - 1401
  • [9] Allogeneic Hematopoietic Stem Cell Transplantation for Adult Patients with Fanconi Anemia.
    Fumani, Hosein Kamranzadeh
    Zokaasadi, Mohammad
    Kasaeian, Amir
    Alimoghaddam, Kamran
    Mousavi, Asadollah
    Bahar, Babak
    Vaezi, Mohammad
    Ghavamzadeh, Ardeshir
    MEDITERRANEAN JOURNAL OF HEMATOLOGY AND INFECTIOUS DISEASES, 2016, 8
  • [10] Novel Manufacturing of Gene Corrected Autologous Blood Stem Cells for Gene Therapy of Fanconi Anemia Complementation Group A
    Adair, Jennifer E.
    Chandrasekaran, Devikha
    Kubek, Sara
    Haworth, Kevin G.
    Becker, Pamela S.
    Woolfrey, Ann E.
    Burroughs, Lauri M.
    Kiem, Hans-Peter
    MOLECULAR THERAPY, 2017, 25 (05) : 40 - 41
12345