ADENO-ASSOCIATED VIRUS VECTOR-MEDIATED LIVER GENE THERAPY FOR CRIGLER-NAJJAR SYNDROME

被引：0
|
作者：
Bosma, P. [1 ]
Labrune, P. [2 ]
Brunetti-Pierri, N. [3 ]
D'Antiga, L. [4 ]
Ott, M. [5 ]
Beinat, M. [6 ]
Ronchi, F. [7 ]
Mavilio, F. [8 ]
Beuers, U. [9 ]
Muro, A. [10 ]
Baumann, U. [5 ]
Mingozzi, F. [8 ]
机构：
[1] Univ Amsterdam, Acad Med Ctr, Liver Ctr, NL-1105 AZ Amsterdam, Netherlands
[2] AP HP, Paris, France
[3] Univ Naples Federico II, Translat Med, Naples, Italy
[4] Azienda Osped Papa Giovanni XXIII, Bergamo, Italy
[5] Hannover Med Sch, Hannover, Germany
[6] Patient Assoc France, Paris, France
[7] CIAMI Onlus, Rimini, Italy
[8] Genethon, Evry, France
[9] Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, Netherlands
[10] Int Ctr Genet Engn & Biotechnol, I-34012 Trieste, Italy
来源：
JOURNAL OF HEPATOLOGY | 2015年 / 62卷
关键词：
D O I：
10.1016/S0168-8278(15)31409-4
中图分类号：
R57 [消化系及腹部疾病];
学科分类号：
摘要：
P1213
引用
收藏
页码：S812 / S812
页数：1
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