ADENO-ASSOCIATED VIRUS VECTOR-MEDIATED LIVER GENE THERAPY FOR CRIGLER-NAJJAR SYNDROME

被引：0

作者：

Bosma, P. ^{[1
]}

Labrune, P. ^{[2
]}

Brunetti-Pierri, N. ^{[3
]}

D'Antiga, L. ^{[4
]}

Ott, M. ^{[5
]}

Beinat, M. ^{[6
]}

Ronchi, F. ^{[7
]}

Mavilio, F. ^{[8
]}

Beuers, U. ^{[9
]}

Muro, A. ^{[10
]}

Baumann, U. ^{[5
]}

Mingozzi, F. ^{[8
]}

机构：

[1] Univ Amsterdam, Acad Med Ctr, Liver Ctr, NL-1105 AZ Amsterdam, Netherlands

[2] AP HP, Paris, France

[3] Univ Naples Federico II, Translat Med, Naples, Italy

[4] Azienda Osped Papa Giovanni XXIII, Bergamo, Italy

[5] Hannover Med Sch, Hannover, Germany

[6] Patient Assoc France, Paris, France

[7] CIAMI Onlus, Rimini, Italy

[8] Genethon, Evry, France

[9] Univ Amsterdam, Acad Med Ctr, NL-1105 AZ Amsterdam, Netherlands

[10] Int Ctr Genet Engn & Biotechnol, I-34012 Trieste, Italy

来源：

JOURNAL OF HEPATOLOGY | 2015年 / 62卷

关键词：

D O I：

10.1016/S0168-8278(15)31409-4

中图分类号：

R57 [消化系及腹部疾病];

学科分类号：

摘要：

P1213

引用

页码：S812 / S812

页数：1

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