Variable clinical features of patients with Fabry disease and outcome of enzyme replacement therapy

被引：0

作者：

Dutra-Clarke, Marina ^{[1
]}

Tapia, Daisy ^{[2
]}

Curtin, Emily ^{[2
]}

Ruenger, Dennis ^{[1
]}

Lakatos, Anita ^{[2
]}

Alandy-Dy, Zyza ^{[2
]}

Freedkin, Linda ^{[2
]}

Hall, Kathy ^{[2
]}

Ercelen, Nesrin ^{[2
]}

Alandy-Dy, Jousef ^{[2
]}

Knight, Margaret ^{[2
]}

Pahl, Madeline ^{[2
]}

Lombardo, Dawn ^{[2
]}

Kimonis, Virginia ^{[2
]}

机构：

[1] Univ Calif Los Angeles, Los Angeles, CA USA

[2] Univ Calif Irvine, Orange, CA 92668 USA

来源：

MOLECULAR GENETICS AND METABOLISM | 2021年 / 132卷 / 02期

关键词：

D O I：

10.1016/j.ymgme.2020.12.069

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：S36 / S36

页数：1

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