Variable clinical features of patients with Fabry disease and outcome of enzyme replacement therapy

被引：0
|
作者：
Dutra-Clarke, Marina [1 ]
Tapia, Daisy [2 ]
Curtin, Emily [2 ]
Ruenger, Dennis [1 ]
Lakatos, Anita [2 ]
Alandy-Dy, Zyza [2 ]
Freedkin, Linda [2 ]
Hall, Kathy [2 ]
Ercelen, Nesrin [2 ]
Alandy-Dy, Jousef [2 ]
Knight, Margaret [2 ]
Pahl, Madeline [2 ]
Lombardo, Dawn [2 ]
Kimonis, Virginia [2 ]
机构：
[1] Univ Calif Los Angeles, Los Angeles, CA USA
[2] Univ Calif Irvine, Orange, CA 92668 USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2021年 / 132卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2020.12.069
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
63
引用
收藏
页码：S36 / S36
页数：1
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