共 50 条
The macrophage as a Trojan horse for antisense oligonucleotide delivery
被引:13
|作者:
Novak, James S.
[1
,2
,3
]
Jaiswal, Jyoti K.
[1
,2
,3
]
Partridge, Terence A.
[1
,2
,3
]
机构:
[1] Childrens Natl Hlth Syst, Childrens Res Inst, Ctr Genet Med Res, Washington, DC USA
[2] George Washington Univ, Sch Med & Hlth Sci, Dept Genom & Precis Med, Washington, DC 20052 USA
[3] George Washington Univ, Sch Med & Hlth Sci, Dept Pediat, Washington, DC 20052 USA
基金:
美国国家卫生研究院;
关键词:
Duchenne muscular dystrophy;
antisense oligonucleotides;
exon skipping;
satellite cells;
macrophages;
drug delivery;
DUCHENNE MUSCULAR-DYSTROPHY;
SYSTEMIC DELIVERY;
MORPHOLINO;
PHARMACOKINETICS;
OLIGOMERS;
EXPRESSION;
SKELETAL;
EFFICACY;
D O I:
10.1080/14728222.2018.1482279
中图分类号:
R9 [药学];
学科分类号:
1007 ;
摘要:
引用
收藏
页码:463 / 466
页数:4
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