The macrophage as a Trojan horse for antisense oligonucleotide delivery

被引:13
|
作者
Novak, James S. [1 ,2 ,3 ]
Jaiswal, Jyoti K. [1 ,2 ,3 ]
Partridge, Terence A. [1 ,2 ,3 ]
机构
[1] Childrens Natl Hlth Syst, Childrens Res Inst, Ctr Genet Med Res, Washington, DC USA
[2] George Washington Univ, Sch Med & Hlth Sci, Dept Genom & Precis Med, Washington, DC 20052 USA
[3] George Washington Univ, Sch Med & Hlth Sci, Dept Pediat, Washington, DC 20052 USA
基金
美国国家卫生研究院;
关键词
Duchenne muscular dystrophy; antisense oligonucleotides; exon skipping; satellite cells; macrophages; drug delivery; DUCHENNE MUSCULAR-DYSTROPHY; SYSTEMIC DELIVERY; MORPHOLINO; PHARMACOKINETICS; OLIGOMERS; EXPRESSION; SKELETAL; EFFICACY;
D O I
10.1080/14728222.2018.1482279
中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
引用
收藏
页码:463 / 466
页数:4
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