DRIVE PK: A Phase 2 Trial of AG-348 in Patients with Pyruvate Kinase Deficiency

被引：0
|
作者：
Barbier, Ann [1 ]
Silver, Bruce [2 ]
Merica, Elizabeth [1 ]
Cohen, Marvin [3 ]
Kung, Charles [1 ]
Yang, Hua [1 ]
Grace, Rachael F. [4 ]
Glader, Bertil [5 ]
Agresta, Sam [1 ]
机构：
[1] Agios Pharmaceut, Cambridge, MA USA
[2] Bruce A Silver Clin Sci & Dev, Dunkirk, MD USA
[3] MBC Pharma Solut, Newtown, PA USA
[4] Harvard Univ, Sch Med, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA
[5] Stanford Univ, Lucile Packard Childrens Hosp, Palo Alto, CA 94304 USA
来源：
BLOOD | 2015年 / 126卷 / 23期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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