DRIVE PK: A Phase 2 Trial of AG-348 in Patients with Pyruvate Kinase Deficiency

被引：0

作者：

Barbier, Ann ^{[1
]}

Silver, Bruce ^{[2
]}

Merica, Elizabeth ^{[1
]}

Cohen, Marvin ^{[3
]}

Kung, Charles ^{[1
]}

Yang, Hua ^{[1
]}

Grace, Rachael F. ^{[4
]}

Glader, Bertil ^{[5
]}

Agresta, Sam ^{[1
]}

机构：

[1] Agios Pharmaceut, Cambridge, MA USA

[2] Bruce A Silver Clin Sci & Dev, Dunkirk, MD USA

[3] MBC Pharma Solut, Newtown, PA USA

[4] Harvard Univ, Sch Med, Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA

[5] Stanford Univ, Lucile Packard Childrens Hosp, Palo Alto, CA 94304 USA

来源：

BLOOD | 2015年 / 126卷 / 23期

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页数：3

共 50 条

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