AAV9-mediated gene therapy in a knock-in mouse model of infantile neuroaxonal dystrophy

被引：0
|
作者：
Whaler, S. [1 ]
Geard, A. F. [1 ]
Poupon-Bejuit, L. [1 ]
Massaro, G. [1 ]
Hughes, M. P. [1 ]
Lalji, K. [1 ]
Waddington, S. N. [1 ,2 ]
Kurian, M. A. [1 ,3 ]
Rahim, A. A. [1 ]
机构：
[1] UCL, London, England
[2] Univ Witwatersrand, Johannesburg, South Africa
[3] Great Ormond St Hosp Sick Children, London, England
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR30
引用
收藏
页码：A12 / A12
页数：1
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