A first-in-human phase 1 clinical gene therapy trial for the treatment of heart failure using a novel rationally designed cardiotropic adeno-associated vector

被引:0
|
作者
Alvisi, Monica [1 ]
Henry, Timothy [2 ]
Chung, Eugene [2 ]
Traverse, Jay [3 ]
Ervin, Leigh [4 ]
Krupa, Shiva [4 ]
Sadek, Hesham [5 ]
Jiang, Canwen [4 ]
Mikhail, Sheila [4 ]
Haghighi, Kobra [6 ]
Kranias, Evangelia [6 ]
Samulski, Jude [4 ]
Tretalova, Anna [4 ]
Hajjar, Roger [7 ]
机构
[1] AskBio, Heidelberg, Germany
[2] Christ Hosp, Cincinnati, OH USA
[3] Minneapolis Heart Inst Fdn, Minneapolis, MN USA
[4] AskBio, Res Triangle Pk, NC USA
[5] UT SouthWestern, Dallas, TX USA
[6] Univ Cincinnati, Cincinnati, OH USA
[7] Flagship Pioneering, Cambridge, MA USA
关键词
D O I
10.1016/j.yjmcc.2022.08.225
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
P271
引用
收藏
页码:S113 / S113
页数:1
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