A first-in-human phase 1 clinical gene therapy trial for the treatment of heart failure using a novel rationally designed cardiotropic adeno-associated vector

被引：0

作者：

Alvisi, Monica ^{[1
]}

Henry, Timothy ^{[2
]}

Chung, Eugene ^{[2
]}

Traverse, Jay ^{[3
]}

Ervin, Leigh ^{[4
]}

Krupa, Shiva ^{[4
]}

Sadek, Hesham ^{[5
]}

Jiang, Canwen ^{[4
]}

Mikhail, Sheila ^{[4
]}

Haghighi, Kobra ^{[6
]}

Kranias, Evangelia ^{[6
]}

Samulski, Jude ^{[4
]}

Tretalova, Anna ^{[4
]}

Hajjar, Roger ^{[7
]}

机构：

[1] AskBio, Heidelberg, Germany

[2] Christ Hosp, Cincinnati, OH USA

[3] Minneapolis Heart Inst Fdn, Minneapolis, MN USA

[4] AskBio, Res Triangle Pk, NC USA

[5] UT SouthWestern, Dallas, TX USA

[6] Univ Cincinnati, Cincinnati, OH USA

[7] Flagship Pioneering, Cambridge, MA USA

来源：

JOURNAL OF MOLECULAR AND CELLULAR CARDIOLOGY | 2022年 / 173卷

关键词：

D O I：

10.1016/j.yjmcc.2022.08.225

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

P271

引用

页码：S113 / S113

页数：1

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