Post-Symptomatic Reversal of Muscle Pathology in a Model of Pompe Disease Using Gene Therapy

被引：0
|
作者：
Ramezani, Ali [1 ]
Hordeaux, Juliette [1 ]
Tuske, Steven [2 ]
Song, Chunjuan [1 ]
Mehta, Nickita [2 ]
Tsai, Patrick [2 ]
Weimer, Jill [2 ]
So, Meardey [1 ]
Bell, Peter [1 ]
Do, Hung [2 ]
Wilson, James M. [1 ]
机构：
[1] Univ Penn, Gene Therapy Program, Philadelphia, PA 19104 USA
[2] Amicus Therapeut Inc, Gene Therapy Ctr Excellence, Philadelphia, PA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
518
引用
收藏
页码：253 / 253
页数：1
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