Post-Symptomatic Reversal of Muscle Pathology in a Model of Pompe Disease Using Gene Therapy

被引：0

作者：

Ramezani, Ali ^{[1
]}

Hordeaux, Juliette ^{[1
]}

Tuske, Steven ^{[2
]}

Song, Chunjuan ^{[1
]}

Mehta, Nickita ^{[2
]}

Tsai, Patrick ^{[2
]}

Weimer, Jill ^{[2
]}

So, Meardey ^{[1
]}

Bell, Peter ^{[1
]}

Do, Hung ^{[2
]}

Wilson, James M. ^{[1
]}

机构：

[1] Univ Penn, Gene Therapy Program, Philadelphia, PA 19104 USA

[2] Amicus Therapeut Inc, Gene Therapy Ctr Excellence, Philadelphia, PA USA

来源：

MOLECULAR THERAPY | 2021年 / 29卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

518

引用

页码：253 / 253

页数：1

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