More is needed to complement the available therapies of spinal muscular atrophy

被引：13

作者：

Singh, Ravindra N. ^{[1
]}

机构：

[1] Iowa State Univ, Dept Biomed Sci, Ames, IA 50011 USA

来源：

FUTURE MEDICINAL CHEMISTRY | 2019年 / 11卷 / 22期

关键词：

AAV9; gene therapy; ISS-N1; nusinersen; oligonucleotide; spinal muscular atrophy (SMA); Spinraza; survival motor neuron (SMN); SURVIVAL MOTOR-NEURON; DISCOVERY; MODIFIER; DISEASE;

D O I：

10.4155/fmc-2019-0239

中图分类号：

R914 [药物化学];

学科分类号：

100701 ;

摘要：

[No abstract available]

引用

页码：2873 / 2876

页数：4

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