More is needed to complement the available therapies of spinal muscular atrophy

被引：13
|
作者：
Singh, Ravindra N. [1 ]
机构：
[1] Iowa State Univ, Dept Biomed Sci, Ames, IA 50011 USA
来源：
FUTURE MEDICINAL CHEMISTRY | 2019年 / 11卷 / 22期
关键词：
AAV9; gene therapy; ISS-N1; nusinersen; oligonucleotide; spinal muscular atrophy (SMA); Spinraza; survival motor neuron (SMN); SURVIVAL MOTOR-NEURON; DISCOVERY; MODIFIER; DISEASE;
D O I：
10.4155/fmc-2019-0239
中图分类号：
R914 [药物化学];
学科分类号：
100701 ;
摘要：
[No abstract available]
引用
收藏
页码：2873 / 2876
页数：4
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