Modeling of aniridia-related keratopathy by CRISPR/Cas9 genome editing of human limbal epithelial cells and rescue by recombinant PAX6 protein

被引：0
|
作者：
Aberdam, D. [1 ]
机构：
[1] Stem Cells & Physiopathol Hop St Louis, INSERM, U976, Paris, France
来源：
ACTA OPHTHALMOLOGICA | 2018年 / 96卷
关键词：
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
3364
引用
收藏
页码：111 / 111
页数：1
相关论文
共 50 条
  • [31] Molecular Dynamics of Genome Editing with CRISPR/Cas9 and rAAV6 Virus in Human HSPCs to Treat Sickle Cell Disease
    Xu, Liwen
    Lahiri, Premanjali
    Skowronski, Jason
    Bhatia, Neehar
    Lattanzi, Annalisa
    Porteus, Matthew H.
    MOLECULAR THERAPY, 2023, 31 (04) : 262 - 263
  • [32] Genome Editing Using CRISPR/Cas9 and rAAV6 to Functionally Correct Wiskott-Aldrich Syndrome in Human HSPCs
    Wiebking, Volker
    Mantri, Sruthi
    Weinberg, Kenneth I.
    Porteus, Matthew H.
    MOLECULAR THERAPY, 2018, 26 (05) : 376 - 377
  • [33] CONDITIONAL REPROGRAMMING SUPPORTS MULTIPOTENT DIFFERENTIATION CAPACITY, CLONING AND CRISPR/CAS9 GENOME EDITING OF PRIMARY CF AND NON-CF HUMAN BRONCHIAL EPITHELIAL CELLS
    Peters-Hall, J. R.
    Coquelin, M. L.
    Torres, M. J.
    LaRanger, R.
    Alabi, B. R.
    Moreno, Calva J. F.
    Thomas, P. J.
    Shay, J. W.
    PEDIATRIC PULMONOLOGY, 2017, 52 : S273 - S273
  • [34] A novel Cas9 fusion protein promotes targeted genome editing with reduced mutational burden in primary human cells
    Carusillo, Antonio
    Haider, Sibtain
    Schaefer, Raul
    Rhiel, Manuel
    Tuerk, Daniel
    Chmielewski, Kay O.
    Klermund, Julia
    Mosti, Laura
    Andrieux, Geoffroy
    Schaefer, Richard
    Cornu, Tatjana, I
    Cathomen, Toni
    Mussolino, Claudio
    NUCLEIC ACIDS RESEARCH, 2023, 51 (09) : 4660 - 4673
  • [35] Decreased FABP5 and DSG1 protein expression following PAX6 knockdown of differentiated human limbal epithelial cells
    Katiyar, Priya
    Stachon, Tanja
    Fries, Fabian N.
    Parow, Frederika
    Ulrich, Myriam
    Langenbucher, Achim
    Cayless, Alan
    Seitz, Berthold
    Kaesmann-Kellner, Barbara
    Latta, Lorenz
    Szentmary, Nora
    EXPERIMENTAL EYE RESEARCH, 2022, 215
  • [36] SliceIt: A genome-wide resource and visualization tool to design CRISPR/Cas9 screens for editing protein-RNA interaction sites in the human genome
    Vemuri, Sasank
    Srivastava, Rajneesh
    Mir, Quoseena
    Hashemikhabir, Seyedsasan
    Dong, X. Charlie
    Janga, Sarath Chandra
    METHODS, 2020, 178 : 104 - 113
  • [37] Comprehensive functional modeling of pan-cancer risk SNP rs6983267 in human CRC cells via scarless CRISPR/Cas9 genome editing
    Coggins, Nicole B.
    O'Geen, Henriette
    Segal, David J.
    Carvajal-Carmona, Luis G.
    CANCER RESEARCH, 2020, 80 (16)
  • [38] Comprehensive functional modeling of pan-cancer risk SNP rs6983267 in human CRC cells via scarless CRISPR/Cas9 genome editing.
    Coggins, Nicole B.
    O'Geen, Henriette
    Segal, David J.
    Carvajal-Carmona, Luis G.
    CANCER RESEARCH, 2020, 80 (11) : 58 - 58
  • [39] Recombinant Cas9 protein production in an endotoxin-free system and evaluation with editing the BCL11A gene in human cells
    Singpant, Passanan
    Tubsuwan, Alisa
    Sakdee, Somsri
    Ketterman, Albert J.
    Jearawiriyapaisarn, Natee
    Kurita, Ryo
    Nakamura, Yukio
    Songdej, Duantida
    Tangprasittipap, Amornrat
    Bhukhai, Kanit
    Chiangjong, Wararat
    Hongeng, Suradej
    Saisawang, Chonticha
    PROTEIN EXPRESSION AND PURIFICATION, 2023, 210
  • [40] CFTR Inactivation by Lentiviral Vector-mediated RNA Interference and CRISPR-Cas9 Genome Editing in Human Airway Epithelial Cells
    Bellec, Jessica
    Bacchetta, Marc
    Losa, Davide
    Anegon, Ignacio
    Chanson, Marc
    Tuan Huy Nguyen
    CURRENT GENE THERAPY, 2015, 15 (05) : 447 - 459
12345