Genome Editing Using CRISPR/Cas9 and rAAV6 to Functionally Correct Wiskott-Aldrich Syndrome in Human HSPCs

被引：0
|
作者：
Wiebking, Volker [1 ]
Mantri, Sruthi [1 ]
Weinberg, Kenneth I. [1 ]
Porteus, Matthew H. [1 ]
机构：
[1] Stanford Univ, Dept Pediat, Stanford, CA 94305 USA
来源：
MOLECULAR THERAPY | 2018年 / 26卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
825
引用
收藏
页码：376 / 377
页数：2
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