AAV6.2: An efficient and safe gene therapy clinical candidate for the treatment of cystic fibrosis airway disease

被引:0
|
作者
Limberis, M. [1 ]
Vandenberghe, L. H. [1 ]
Zhang, L. [2 ]
Pickles, R. J. [2 ]
Wilson, J. M. [1 ]
机构
[1] Univ Penn, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA
[2] Univ N Carolina, Csyt Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27515 USA
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R72 [儿科学];
学科分类号
100202 ;
摘要
273
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页码:298 / 298
页数:1
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