Development of a Clinically-Acceptable Lentiviral Vector for Cystic Fibrosis Airway Gene Therapy

被引:0
|
作者
McCarron, Alexandra [1 ]
McIntyre, Chantelle [2 ]
Donnelley, Martin [2 ]
Cmielewski, Patricia [3 ]
Parsons, David [3 ]
机构
[1] Univ Adelaide, Sch Med, Adelaide, SA, Australia
[2] Univ Adelaide, Robinson Res Inst, Adelaide, SA, Australia
[3] Womens & Childrens Hosp, Resp & Sleep Med, Adelaide, SA, Australia
关键词
D O I
10.1016/S1525-0016(16)33519-5
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
711
引用
收藏
页码:S280 / S281
页数:2
相关论文
共 50 条
  • [1] LENTIVIRAL VECTOR OPTIMIZATION FOR CYSTIC FIBROSIS GENE THERAPY
    Loza, Marquez L., I
    Cooney, A. L.
    Sinn, P.
    McCray, P. B., Jr.
    PEDIATRIC PULMONOLOGY, 2020, 55 : S239 - S240
  • [2] Lentiviral vector gene therapy and CFTR modulators show comparable effectiveness in cystic fibrosis rat airway models
    Mccarron, Alexandra
    Ling, Kak-Ming
    Montgomery, Samuel T.
    Martinovich, Kelly M.
    Cmielewski, Patricia
    Rout-Pitt, Nathan
    Kicic, Anthony
    Parsons, David
    Donnelley, Martin
    GENE THERAPY, 2024, 31 (11-12) : 553 - 559
  • [3] Lentiviral vectors for gene therapy of cystic fibrosis
    Goldman, MJ
    Lee, PS
    Yang, JS
    Wilson, JM
    HUMAN GENE THERAPY, 1997, 8 (18) : 2261 - 2268
  • [4] Lentiviral Vectors and Cystic Fibrosis Gene Therapy
    Castellani, Stefano
    Conese, Massimo
    VIRUSES-BASEL, 2010, 2 (02): : 395 - 412
  • [5] Lentiviral Airway Gene Therapy Correction of CFTR Function in Knockout Cystic Fibrosis Rats
    Reyne, Nikki
    Cmielewski, Patricia
    McCarron, Alexandra
    Parsons, David
    Donnelley, Martin
    MOLECULAR THERAPY, 2021, 29 (04) : 259 - 259
  • [6] Airway gene therapy and cystic fibrosis
    Parsons, DW
    JOURNAL OF PAEDIATRICS AND CHILD HEALTH, 2005, 41 (03) : 94 - 96
  • [7] DEVELOPMENT OF ASSAYS TO ASSESS SAFETY AND EFFICACY OF LENTIVIRAL GENE THERAPY FOR CYSTIC FIBROSIS
    Saleh, A. D.
    Clarke, N. K.
    Meng, C.
    Jacobson, M. R.
    Davies, J. C.
    Durham, S. R.
    Alton, E. W. F. W.
    Griesenbach, U.
    THORAX, 2017, 72 : A57 - A57
  • [8] Increased CFTR expression and function from an optimized lentiviral vector for cystic fibrosis gene therapy
    Loza, Laura I. Marquez
    Cooney, Ashley L.
    Dong, Qian
    Randak, Christoph O.
    Rivella, Stefano
    Sinn, Patrick L.
    McCray, Paul B., Jr.
    MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2021, 21 : 94 - 106
  • [9] IMPROVING THE TRANSDUCTION EFFICIENCY OF AN AEROSOL DELIVERED LENTIVIRAL VECTOR FOR CYSTIC FIBROSIS LUNG GENE THERAPY
    Padmanabhan, Harshavardini
    Cmielewski, Patricia
    Donnelley, Martin
    Parsons, David
    JOURNAL OF AEROSOL MEDICINE AND PULMONARY DRUG DELIVERY, 2014, 27 (06) : A7 - A7
  • [10] Development of a Clinically-Applicable Lentiviral Vector for RS-SCID Gene Therapy
    Charrier, Sabine
    Cedrone, Gregory
    Lagresle, Chantal
    Cacavelli, Laure
    Sanatine, Peggy
    De Villartay, Jean-Pierre
    Cavazzana-Calvo, Marina
    Abina, Salima Hacein-Bey
    Galy, Anne
    MOLECULAR THERAPY, 2012, 20 : S88 - S89