SYSTEMATIC LITERATURE REVIEW ON THE WORLDWIDE EPIDEMIOLOGY OF METHYLMALONIC ACIDEMIA WITH A FOCUS ON METHYLMALONYL-COA MUTASE DEFICIENCY

被引：0

作者：

Almasi, T. ^{[1
]}

Guey, L. ^{[2
]}

Lukacs, C. ^{[2
]}

Csetneki, K. ^{[1
]}

Voko, Z. ^{[1
]}

Zelei, T. ^{[1
]}

机构：

[1] Syreon Res Inst, Budapest, Hungary

[2] Moderna Therapeut, Cambridge, MA USA

来源：

VALUE IN HEALTH | 2018年 / 21卷

关键词：

D O I：

10.1016/j.jval.2018.09.2612

中图分类号：

F [经济];

学科分类号：

02 ;

摘要：

PSY35

引用

页码：S441 / S441

页数：1

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