SYSTEMATIC LITERATURE REVIEW ON THE WORLDWIDE EPIDEMIOLOGY OF METHYLMALONIC ACIDEMIA WITH A FOCUS ON METHYLMALONYL-COA MUTASE DEFICIENCY

被引：0
|
作者：
Almasi, T. [1 ]
Guey, L. [2 ]
Lukacs, C. [2 ]
Csetneki, K. [1 ]
Voko, Z. [1 ]
Zelei, T. [1 ]
机构：
[1] Syreon Res Inst, Budapest, Hungary
[2] Moderna Therapeut, Cambridge, MA USA
来源：
VALUE IN HEALTH | 2018年 / 21卷
关键词：
D O I：
10.1016/j.jval.2018.09.2612
中图分类号：
F [经济];
学科分类号：
02 ;
摘要：
PSY35
引用
收藏
页码：S441 / S441
页数：1
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