Treatment of Aged Mice and Long-Term Durability of AAV-Mediated Gene Therapy in Two Mouse Models of LGMD

被引:0
|
作者
Pozsgai, Eric R. [1 ]
Griffin, Danielle A. [1 ]
Peterson, Ellyn L. [1 ]
Kempton, Amber [1 ]
Rogers, Oliver [1 ]
Seo, Young-Eun [1 ]
Rodino-Klapac, Louise R. [1 ]
机构
[1] Sarepta Therapeut Inc, Cambridge, MA USA
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中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1137
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页码:491 / 491
页数:1
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