Treatment of Aged Mice and Long-Term Durability of AAV-Mediated Gene Therapy in Two Mouse Models of LGMD

被引：0
|
作者：
Pozsgai, Eric R. [1 ]
Griffin, Danielle A. [1 ]
Peterson, Ellyn L. [1 ]
Kempton, Amber [1 ]
Rogers, Oliver [1 ]
Seo, Young-Eun [1 ]
Rodino-Klapac, Louise R. [1 ]
机构：
[1] Sarepta Therapeut Inc, Cambridge, MA USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1137
引用
收藏
页码：491 / 491
页数：1
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