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- [1] Neonatal gene transfer using lentiviral vector for murine Pompe disease: long-term expression and glycogen reduction[J]. GENE THERAPY, 2010, 17 (04) : 521 - 530Kyosen, S. O.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanIizuka, S.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanKobayashi, H.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Pediat, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Genet Dis, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanKimura, T.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Urol, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanFukuda, T.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Div Neuropathol, Sch Med, Res Ctr Med Sci,Dept Neurosci, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanShen, J.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Genet Dis, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanShimada, Y.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanIda, H.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Pediat, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Genet Dis, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanEto, Y.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Pediat, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Genet Dis, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, JapanOhashi, T.论文数: 0 引用数: 0 h-index: 0机构: Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, Japan Jikei Univ, Dept Pediat, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Genet Dis, Sch Med, Tokyo 1058461, Japan Jikei Univ, Dept Gene Therapy, Inst DNA Med, Sch Med,Minato Ku, Tokyo 1058461, Japan
- [2] Neonatal gene transfer using lentiviral vector for murine Pompe disease: long-term expression and glycogen reduction[J]. Gene Therapy, 2010, 17 : 521 - 530S O Kyosen论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyS Iizuka论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyH Kobayashi论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyT Kimura论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyT Fukuda论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyJ Shen论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyY Shimada论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyH Ida论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyY Eto论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene TherapyT Ohashi论文数: 0 引用数: 0 h-index: 0机构: Institute of DNA Medicine,Department of Gene Therapy
- [3] Ex Vivo Lentiviral Gene Therapy as a Cure for Murine Pompe Disease[J]. MOLECULAR THERAPY, 2013, 21 : S105 - S105Stok, Merel论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, Netherlandsde Boer, Helen论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsHuston, Marshall W.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsJacobs, Edwin H.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsRoovers, Onno论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsJahr, Holger论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsDuncker, Dirk J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsVisser, Trudi P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, Netherlandsvan der Ploeg, Ans T.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Ctr Lysosomal & Metab Dis, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsReuser, Arnold J. J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Ctr Lysosomal & Metab Dis, Rotterdam, Netherlands Erasmus MC, Rotterdam, Netherlandsvan Til, Nico P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, NetherlandsWagemaker, Gerard论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, Rotterdam, Netherlands Erasmus MC, Rotterdam, Netherlands
- [4] Lentiviral gene therapy for Pompe disease[J]. HUMAN GENE THERAPY, 2011, 22 (10) : A40 - A41Stok, M.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlandsde Boer, H.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlandsde Visser, T. P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, NetherlandsReuser, A. J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Dept Clin Genet, Med Ctr, NL-3000 DR Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, NetherlandsJacobs, E.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Dept Genet, Med Ctr, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, NetherlandsJahr, H.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Dept Orthoped, Med Ctr, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, NetherlandsDuncker, D.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Dept Expt Cardiol, Med Ctr, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlandsvan Til, N. P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, NetherlandsWagemaker, G.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, Rotterdam, Netherlands
- [5] Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease[J]. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2020, 17 : 1014 - 1025Stok, Merel论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Pediat, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Ctr Lysosomal & Metab Dis, Rotterdam, Netherlands ProPharma Grp, Leiden, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlandsde Boer, Helen论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Clin Genet, Mol Stem Cell Biol, Rotterdam, Netherlands Merus NV, Utrecht, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsHuston, Marshall W.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Mol Genet, Rotterdam, Netherlands Sangamo Therapeut, Richmond, CA USA Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsJacobs, Edwin H.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Mol Genet, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Clin Genet, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsRoovers, Onno论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsVisser, Trudi P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsJahr, Holger论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Orthopaed, Rotterdam, Netherlands Univ Hosp RWTH, Dept Orthopaed, Aachen, Germany Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsDuncker, Dirk J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Cardiol, Div Expt Cardiol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlandsvan Deel, Elza D.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Cardiol, Div Expt Cardiol, Rotterdam, Netherlands Rotterdam Univ Appl Sci, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsReuser, Arnold J. J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Ctr Lysosomal & Metab Dis, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Clin Genet, Mol Stem Cell Biol, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlandsvan Til, Niek P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Univ Med Ctr Utrecht, Ctr Translat Immunol, Cambridge, MA USA AvroBio, Cambridge, MA USA Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, NetherlandsWagemaker, Gerard论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands Hacettepe Med Univ, Stem Cell Res & Dev Ctr, Ankara, Turkey First Pavlov State Med Univ, Raisa Gorbacheva Mem Res Inst Pediat Oncol & Hema, St Petersburg, Russia Erasmus Univ, Med Ctr, Dept Hematol, POB 37048, NL-3005 LA Rotterdam, Netherlands
- [6] Lentiviral gene therapy of murine hematopoietic stem cells ameliorates the Pompe disease phenotype[J]. BLOOD, 2010, 115 (26) : 5329 - 5337van Til, Niek P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsStok, Merel论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsKaya, Fatima S. F. Aerts论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlandsde Waard, Monique C.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Expt Cardiol, Dept Cardiol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsFarahbakhshian, Elnaz论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsVisser, Trudi P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsKroos, Marian A.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Clin Genet, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsJacobs, Edwin H.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Cell Biol & Genet, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsWillart, Monique A.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Pulm Med, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlandsvan der Wegen, Pascal论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Cell Biol & Genet, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsScholte, Bob J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Cell Biol & Genet, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsLambrecht, Bart N.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Pulm Med, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsDuncker, Dirk J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Expt Cardiol, Dept Cardiol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlandsvan der Ploeg, Ans T.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Med Ctr Sophia, Dept Pediat, Div Metab Dis & Genet, Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsReuser, Arnold J. J.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Clin Genet, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsVerstegen, Monique M.论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, NetherlandsWagemaker, Gerard论文数: 0 引用数: 0 h-index: 0机构: Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands Erasmus Univ, Med Ctr, Dept Hematol, NL-3015 GE Rotterdam, Netherlands
- [7] Lentiviral stem cell gene therapy for Pompe disease[J]. HUMAN GENE THERAPY, 2014, 25 (11) : A62 - A63Liang, Qiushi论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, Netherlandsvan Helsdingen, Yvette论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, Netherlandsvan der Velden, Guus论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsStok, Merel论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsJacobs, Ed论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsDuncker, Dirk论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsReuser, Arnold论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, Netherlandsvan der Ploeg, Ans论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsVulto, Arnold论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, Netherlandsvan Til, Niek P.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC, NL-3015 CE Rotterdam, Netherlands Erasmus MC, NL-3015 CE Rotterdam, NetherlandsWagemaker, Gerard论文数: 0 引用数: 0 h-index: 0机构: Hacettepe Univ, Stem Cell Res Ctr, TR-06100 Ankara, Turkey Erasmus MC, NL-3015 CE Rotterdam, Netherlands
- [8] LENTIVIRAL GENE THERAPY OF MURINE HEMATOPOIETIC STEM CELLS LEADS TO CORRECTION OF THE POMPE DISEASE PHENOTYPE[J]. CLINICAL THERAPEUTICS, 2010, 32 : S81 - S81Stok, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlandsvan Til, N. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsKaya, F. S. F. Aerts论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsFarahbakhshian, E.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsVisser, T. P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsKroos, M. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Clin Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlandsde Waard, M. C.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Cardiol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsJacobs, E. H.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Cell Biol & Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsWillart, M. A.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Pulm Med, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlandsvan der Wegen, P.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Cell Biol & Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsScholte, B. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Cell Biol & Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsLambrecht, B. N.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Pulm Med, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsDuncker, D. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Cardiol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlandsvan der Ploeg, A. T.论文数: 0 引用数: 0 h-index: 0机构: Erasmus MC Sopbia, Dept Pediat, Div Metab Dis & Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsReuser, A. J. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Clin Genet, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsVerstegen, M. V.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, NetherlandsWagemaker, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands
- [9] Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease[J]. MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2020, 18 : 558 - 570Piras, Giuseppa论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandMontiel-Equihua, Claudia论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandChan, Yee-Ka Agnes论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandWantuch, Slawomir论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandStuckey, Daniel论文数: 0 引用数: 0 h-index: 0机构: UCL, Ctr Adv Biomed Imaging, London WC1E 6DD, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandBurke, Derek论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hos, Enzyme & Metab Lab, London WC1N 3JH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandPrunty, Helen论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hos, Enzyme & Metab Lab, London WC1N 3JH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandPhadke, Rahul论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, MRC Ctr Neuromuscular Dis, Dubowitz Neuromuscular Ctr, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandChambers, Darren论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, MRC Ctr Neuromuscular Dis, Dubowitz Neuromuscular Ctr, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandPartida-Gaytan, Armando论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England Fdn Mexicana Ninas & Ninos Con Inmunodeficiencias, Ciudad De Mexico, Mexico UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandLeon-Rico, Diego论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandPanchal, Neelam论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandWhitmore, Kathryn论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandCalero, Miguel论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandBenedetti, Sara论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England NIHR Great Ormond St Hosp Biomed Res Ctr, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandSantilli, Giorgia论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England NIHR Great Ormond St Hosp Biomed Res Ctr, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, EnglandGaspar, H. Bobby论文数: 0 引用数: 0 h-index: 0机构: UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England Orchard Therapeut Ltd, London EC4N 6EU, England UCL, UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Sect, Infect Immun & Inflammat Program, 30 Guilford St, London WC1N 1EH, England
- [10] Long term pulmonary gene therapy with a lentiviral vector in a fetal rat model[J]. AMERICAN JOURNAL OF OBSTETRICS AND GYNECOLOGY, 2006, 195 (06) : S22 - S22Toelen, Jaan论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, BelgiumRik, Gijsbers论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, BelgiumSbragia, Loureco论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, BelgiumChristophe, Deroose论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, BelgiumDebyser, Zeger论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, BelgiumDeprest, Jan论文数: 0 引用数: 0 h-index: 0机构: Catholic Univ Louvain, B-3000 Louvain, Belgium