LENTIVIRAL GENE THERAPY OF MURINE HEMATOPOIETIC STEM CELLS LEADS TO CORRECTION OF THE POMPE DISEASE PHENOTYPE

被引：0

作者：

Stok, M. ^{[1
]}

van Til, N. P. ^{[1
]}

Kaya, F. S. F. Aerts ^{[1
]}

Farahbakhshian, E. ^{[1
]}

Visser, T. P. ^{[1
]}

Kroos, M. A. ^{[2
]}

de Waard, M. C. ^{[3
]}

Jacobs, E. H. ^{[4
]}

Willart, M. A. ^{[5
]}

van der Wegen, P. ^{[4
]}

Scholte, B. J. ^{[4
]}

Lambrecht, B. N. ^{[5
]}

Duncker, D. J. ^{[3
]}

van der Ploeg, A. T. ^{[6
]}

Reuser, A. J. J. ^{[2
]}

Verstegen, M. V. ^{[1
]}

Wagemaker, G. ^{[1
]}

机构：

[1] Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands

[2] Univ Med Ctr, Erasmus MC, Dept Clin Genet, Rotterdam, Netherlands

[3] Univ Med Ctr, Erasmus MC, Dept Cardiol, Rotterdam, Netherlands

[4] Univ Med Ctr, Erasmus MC, Dept Cell Biol & Genet, Rotterdam, Netherlands

[5] Univ Med Ctr, Erasmus MC, Dept Pulm Med, Rotterdam, Netherlands

[6] Erasmus MC Sopbia, Dept Pediat, Div Metab Dis & Genet, Rotterdam, Netherlands

来源：

CLINICAL THERAPEUTICS | 2010年 / 32卷

关键词：

D O I：

暂无

中图分类号：

R9 [药学];

学科分类号：

1007 ;

摘要：

引用

页码：S81 / S81

页数：1

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[1] Lentiviral gene therapy of murine hematopoietic stem cells ameliorates the Pompe disease phenotype
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[2] LENTIVIRAL GENE THERAPY OF HEMATOPOIETIC STEM CELLS RESULTS IN PHENOTYPE CORRECTION IN A MOUSE MODEL OF POMPE DISEASE
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