LENTIVIRAL GENE THERAPY OF MURINE HEMATOPOIETIC STEM CELLS LEADS TO CORRECTION OF THE POMPE DISEASE PHENOTYPE

被引:0
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作者
Stok, M. [1 ]
van Til, N. P. [1 ]
Kaya, F. S. F. Aerts [1 ]
Farahbakhshian, E. [1 ]
Visser, T. P. [1 ]
Kroos, M. A. [2 ]
de Waard, M. C. [3 ]
Jacobs, E. H. [4 ]
Willart, M. A. [5 ]
van der Wegen, P. [4 ]
Scholte, B. J. [4 ]
Lambrecht, B. N. [5 ]
Duncker, D. J. [3 ]
van der Ploeg, A. T. [6 ]
Reuser, A. J. J. [2 ]
Verstegen, M. V. [1 ]
Wagemaker, G. [1 ]
机构
[1] Univ Med Ctr, Erasmus MC, Dept Hematol, Rotterdam, Netherlands
[2] Univ Med Ctr, Erasmus MC, Dept Clin Genet, Rotterdam, Netherlands
[3] Univ Med Ctr, Erasmus MC, Dept Cardiol, Rotterdam, Netherlands
[4] Univ Med Ctr, Erasmus MC, Dept Cell Biol & Genet, Rotterdam, Netherlands
[5] Univ Med Ctr, Erasmus MC, Dept Pulm Med, Rotterdam, Netherlands
[6] Erasmus MC Sopbia, Dept Pediat, Div Metab Dis & Genet, Rotterdam, Netherlands
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中图分类号
R9 [药学];
学科分类号
1007 ;
摘要
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页码:S81 / S81
页数:1
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