Ex Vivo Lentiviral Gene Therapy as a Cure for Murine Pompe Disease

被引：0
|
作者：
Stok, Merel [1 ]
de Boer, Helen [1 ]
Huston, Marshall W. [1 ]
Jacobs, Edwin H. [1 ]
Roovers, Onno [1 ]
Jahr, Holger [1 ]
Duncker, Dirk J. [1 ]
Visser, Trudi P. [1 ]
van der Ploeg, Ans T. [2 ]
Reuser, Arnold J. J. [2 ]
van Til, Nico P. [1 ]
Wagemaker, Gerard [1 ]
机构：
[1] Erasmus MC, Rotterdam, Netherlands
[2] Erasmus MC, Ctr Lysosomal & Metab Dis, Rotterdam, Netherlands
来源：
MOLECULAR THERAPY | 2013年 / 21卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
275
引用
收藏
页码：S105 / S105
页数：1
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