Generation of transplantable cells for ex vivo gene therapy of globoid cell leukodystrophy (Krabbe disease).

被引：0
|
作者：
Rafi, MA [1 ]
Zaka, M [1 ]
Rao, HZ [1 ]
Luzi, P [1 ]
Wenger, DA [1 ]
机构：
[1] Thomas Jefferson Univ, Dept Neurol, Philadelphia, PA 19107 USA
来源：
AMERICAN JOURNAL OF HUMAN GENETICS | 2001年 / 69卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q3 [遗传学];
学科分类号：
071007 ; 090102 ;
摘要：
2926
引用
收藏
页码：679 / 679
页数：1
相关论文
共 50 条
  • [41] INTRACEREBRAL PARAVENTRICULAR HYPERDENSITIES - A NEW CT SIGN IN KRABBE GLOBOID-CELL LEUKODYSTROPHY
    FEANNY, SJ
    CHUANG, SH
    BECKER, LE
    CLARKE, JTR
    JOURNAL OF INHERITED METABOLIC DISEASE, 1987, 10 (01) : 24 - 27
  • [42] An ex vivo gene therapy approach for metachromatic leukodystrophy using neural progenitor cells
    Kawabata, K
    Migita, M
    Mochizuki, H
    Fukunaga, Y
    Shimada, T
    MOLECULAR THERAPY, 2004, 9 : S329 - S329
  • [43] Adult onset globoid cell leukodystrophy (Krabbe disease): analysis of galactosylceramidase cDNA from four Japanese patients
    Furuya, H
    Kukita, YJ
    Nagano, S
    Sakai, Y
    Yamashita, Y
    Fukuyama, H
    Inatomi, Y
    Saito, Y
    Koike, R
    Tsuji, S
    Fukumaki, Y
    Hayashi, K
    Kobayashi, T
    HUMAN GENETICS, 1997, 100 (3-4) : 450 - 456
  • [44] Allogeneic MSD-Bone Marrow Tranplantation in Globoid Cell Leukodystrophy (Krabbe's disease) in a Small Infant
    Salvador, C.
    Crazzolara, R.
    Meister, B.
    Kropshofer, G.
    BONE MARROW TRANSPLANTATION, 2015, 50 : 5616 - 5617
  • [45] LATE-ONSET KRABBE DISEASE (GLOBOID-CELL LEUKODYSTROPHY) - CLINICAL AND BIOCHEMICAL FEATURES OF 15 CASES
    KOLODNY, EH
    RAGHAVAN, S
    KRIVIT, W
    DEVELOPMENTAL NEUROSCIENCE, 1991, 13 (4-5) : 232 - 239
  • [46] Delivery of Galactocerebrosidase Activity to the Peripheral Nervous System of Mice with Globoid Cell Leukodystrophy (Krabbe Disease) by Intramuscular Injection
    Rafi, Mohammad A.
    Rao, Han Zhi
    Luzi, Paola
    Curtis, Mark T.
    Wenger, David A.
    MOLECULAR THERAPY, 2006, 13 : S82 - S82
  • [47] Ex vivo cell-mediated gene therapy for metachromatic leukodystrophy using neurospheres
    Kawabata, Ken
    Migita, Makoto
    Mochizuki, Hideki
    Miyake, Koichi
    Igarashi, Tsutomu
    Fukunaga, Yoshitaka
    Shimada, Takashi
    BRAIN RESEARCH, 2006, 1094 : 13 - 23
  • [48] KRABBES DISEASE - GLOBOID-CELL LEUKODYSTROPHY
    JACOB, JC
    KUTTY, KM
    ISLAM, M
    DOMINIC, RG
    DAWSON, G
    CANADIAN MEDICAL ASSOCIATION JOURNAL, 1973, 108 (11) : 1398 - 1400
  • [49] Siblings with Krabbe disease lacking globoid cells.
    Del Bigio, MR
    JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY, 2001, 60 (05): : 557 - 557
  • [50] ULTRASTRUCTURE OF GLOBOID LEUKODYSTROPHY (KRABBES DISEASE) WITH REFERENCE TO ORIGIN OF GLOBOID CELLS
    LIU, HM
    JOURNAL OF NEUROPATHOLOGY AND EXPERIMENTAL NEUROLOGY, 1970, 29 (03): : 441 - &
12345