Generation of transplantable cells for ex vivo gene therapy of globoid cell leukodystrophy (Krabbe disease).

被引：0
|
作者：
Rafi, MA [1 ]
Zaka, M [1 ]
Rao, HZ [1 ]
Luzi, P [1 ]
Wenger, DA [1 ]
机构：
[1] Thomas Jefferson Univ, Dept Neurol, Philadelphia, PA 19107 USA
来源：
AMERICAN JOURNAL OF HUMAN GENETICS | 2001年 / 69卷 / 04期
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D O I：
暂无
中图分类号：
Q3 [遗传学];
学科分类号：
071007 ; 090102 ;
摘要：
2926
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页码：679 / 679
页数：1
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