Clinical outcome study in dysferlinopathy: medical comorbidities and polytherapy in a large population of dysferlinopathy patients

被引：0
|
作者：
Fernandez-Torron, R. [1 ]
Diaz-Manera, J. [2 ]
James, M. [3 ]
Mayhew, A. [3 ]
Spuler, S. [4 ]
Day, J. [5 ]
Jones, K. [6 ]
Bharucha-Goebel, D. [7 ]
Salort-Campana, E. [8 ]
Pestronk, A. [9 ]
Walter, M. [10 ]
Paradas, C. [11 ]
Stojkovic, T. [12 ]
Mori-Yoshimura, M. [13 ]
Bravver, E. [14 ]
Pegoraro, E. [15 ]
Mendell, J. [16 ]
Bushby, K. [3 ]
Straub, V. [3 ]
机构：
[1] Hosp Donostia, Donostia San Sebastian, Spain
[2] Hosp Santa Creu & Sant Pau, Barcelona, Spain
[3] John Walton Muscular Dystrophy, Newcastle Upon Tyne, Tyne & Wear, England
[4] Charite Med Fac, Berlin, Germany
[5] Stanford Univ, Stanford, CA 94305 USA
[6] Westmead Childrens Hosp, Sydney, NSW, Australia
[7] Childrens Natl Hlth, Washington, DC USA
[8] La Timone Hosp, Marseille, France
[9] Washington Univ, St Louis, MO USA
[10] Univ Munich, Munich, Germany
[11] Hosp Univ Virgen del Rocio, Seville, Spain
[12] Inst Myol, Paris, France
[13] NCNP, Tokyo, Japan
[14] Carolinas Healthcare, Charlotte, NC USA
[15] Univ Padua, Padua, Italy
[16] Nationwide Childrens Hosp, Columbus, OH USA
[17] Jain Consortium, Seattle, WA USA
来源：
NEUROMUSCULAR DISORDERS | 2018年 / 28卷
关键词：
D O I：
10.1016/j.nmd.2018.06.041
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
P.12
引用
收藏
页码：S35 / S35
页数：1
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