Clinical outcome study in dysferlinopathy: medical comorbidities and polytherapy in a large population of dysferlinopathy patients

被引：0

作者：

Fernandez-Torron, R. ^{[1
]}

Diaz-Manera, J. ^{[2
]}

James, M. ^{[3
]}

Mayhew, A. ^{[3
]}

Spuler, S. ^{[4
]}

Day, J. ^{[5
]}

Jones, K. ^{[6
]}

Bharucha-Goebel, D. ^{[7
]}

Salort-Campana, E. ^{[8
]}

Pestronk, A. ^{[9
]}

Walter, M. ^{[10
]}

Paradas, C. ^{[11
]}

Stojkovic, T. ^{[12
]}

Mori-Yoshimura, M. ^{[13
]}

Bravver, E. ^{[14
]}

Pegoraro, E. ^{[15
]}

Mendell, J. ^{[16
]}

Bushby, K. ^{[3
]}

Straub, V. ^{[3
]}

机构：

[1] Hosp Donostia, Donostia San Sebastian, Spain

[2] Hosp Santa Creu & Sant Pau, Barcelona, Spain

[3] John Walton Muscular Dystrophy, Newcastle Upon Tyne, Tyne & Wear, England

[4] Charite Med Fac, Berlin, Germany

[5] Stanford Univ, Stanford, CA 94305 USA

[6] Westmead Childrens Hosp, Sydney, NSW, Australia

[7] Childrens Natl Hlth, Washington, DC USA

[8] La Timone Hosp, Marseille, France

[9] Washington Univ, St Louis, MO USA

[10] Univ Munich, Munich, Germany

[11] Hosp Univ Virgen del Rocio, Seville, Spain

[12] Inst Myol, Paris, France

[13] NCNP, Tokyo, Japan

[14] Carolinas Healthcare, Charlotte, NC USA

[15] Univ Padua, Padua, Italy

[16] Nationwide Childrens Hosp, Columbus, OH USA

[17] Jain Consortium, Seattle, WA USA

来源：

NEUROMUSCULAR DISORDERS | 2018年 / 28卷

关键词：

D O I：

10.1016/j.nmd.2018.06.041

中图分类号：

R74 [神经病学与精神病学];

学科分类号：

摘要：

P.12

引用

页码：S35 / S35

页数：1

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