Evaluating the effect of long-term idebenone treatment on respiratory morbidity in patients with Duchenne muscular dystrophy (DMD)

被引：3
|
作者：
Mayer, Oscar Henry [1 ]
Leinonen, Mika [2 ]
Servais, Laurent [3 ]
Straathof, Chiara [4 ]
Schara, Ulrike [5 ]
Voit, Thomas [6 ]
Mercuri, Eugenio [7 ]
Buyse, Gunnar [8 ]
机构：
[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA
[2] Santhera Pharmaceut, Pratteln, Switzerland
[3] CHU Liege, Ctr Reference Neuromusculaire, Liege, Belgium
[4] Leiden Univ, Med Ctr, Leiden, Netherlands
[5] Univ Klinikum Essen, Zentrum Kinderheilikunde Sozialpadiatr Zentrum, Essen, Germany
[6] UCL Great Ormond St Inst Child Hlth, NIHR Great Ormond St Hosp Biomed Res Ctr, London, England
[7] Catholic Univ, Paediat Neurol Unit, Rome, Italy
[8] Univ Hosp Leuven, Leuven, Belgium
来源：
EUROPEAN RESPIRATORY JOURNAL | 2019年 / 54卷
关键词：
Neuromuscular diseases;
D O I：
10.1183/13993003.congress-2019.OA5330
中图分类号：
R56 [呼吸系及胸部疾病];
学科分类号：
摘要：
OA5330
引用
收藏
页数：2
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