Evaluating the effect of long-term idebenone treatment on respiratory morbidity in patients with Duchenne muscular dystrophy (DMD)

被引：3

作者：

Mayer, Oscar Henry ^{[1
]}

Leinonen, Mika ^{[2
]}

Servais, Laurent ^{[3
]}

Straathof, Chiara ^{[4
]}

Schara, Ulrike ^{[5
]}

Voit, Thomas ^{[6
]}

Mercuri, Eugenio ^{[7
]}

Buyse, Gunnar ^{[8
]}

机构：

[1] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[2] Santhera Pharmaceut, Pratteln, Switzerland

[3] CHU Liege, Ctr Reference Neuromusculaire, Liege, Belgium

[4] Leiden Univ, Med Ctr, Leiden, Netherlands

[5] Univ Klinikum Essen, Zentrum Kinderheilikunde Sozialpadiatr Zentrum, Essen, Germany

[6] UCL Great Ormond St Inst Child Hlth, NIHR Great Ormond St Hosp Biomed Res Ctr, London, England

[7] Catholic Univ, Paediat Neurol Unit, Rome, Italy

[8] Univ Hosp Leuven, Leuven, Belgium

来源：

EUROPEAN RESPIRATORY JOURNAL | 2019年 / 54卷

关键词：

Neuromuscular diseases;

D O I：

10.1183/13993003.congress-2019.OA5330

中图分类号：

R56 [呼吸系及胸部疾病];

学科分类号：

摘要：

OA5330

引用

页数：2

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