Gene therapy goes the distance in Wiskott-Aldrich syndrome

被引：1

作者：

Biffi, Alessandra ^{[1
,2
]}

机构：

[1] Padua Univ Hosp, Pediat Hematol Oncol & Stem Cell Transplant Div, Padua, Italy

[2] Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA 02115 USA

来源：

关键词：

EFFICACY;

D O I：

10.1038/s41591-021-01653-7

中图分类号：

Q5 [生物化学]; Q7 [分子生物学];

学科分类号：

071010 ; 081704 ;

摘要：

Long-term follow-up data reinforce the curative potential of hematopoietic stem-cell gene therapy for this rare primary immunodeficiency disorder.

引用

页码：24 / 25

页数：2

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