Gene therapy goes the distance in Wiskott-Aldrich syndrome

被引：1
|
作者：
Biffi, Alessandra [1 ,2 ]
机构：
[1] Padua Univ Hosp, Pediat Hematol Oncol & Stem Cell Transplant Div, Padua, Italy
[2] Dana Farber Boston Childrens Canc & Blood Disorde, Gene Therapy Program, Boston, MA 02115 USA
来源：
NATURE MEDICINE | 2022年 / 28卷 / 01期
关键词：
EFFICACY;
D O I：
10.1038/s41591-021-01653-7
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
Long-term follow-up data reinforce the curative potential of hematopoietic stem-cell gene therapy for this rare primary immunodeficiency disorder.
引用
收藏
页码：24 / 25
页数：2
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