Gene therapy of murine GM1 gangliosidosis by genetically modified bone marrow hematopoietic progenitor cells.

被引:0
|
作者
Sano, R [1 ]
Tessitore, A [1 ]
Mann, L [1 ]
d'Azzo, A [1 ]
机构
[1] St Jude Childrens Res Hosp, Memphis, TN 38105 USA
关键词
D O I
暂无
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
2693
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页码:627 / 627
页数:1
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