Gene Therapy for GM1 Gangliosidosis Mediated by AAV Vector Carrying BBB-Penetrable Enzyme

被引：0

作者：

Matsushima, Saki ^{[1
]}

Iizuka, Sayoko ^{[1
]}

Kinoshita, Masafumi ^{[2
]}

Takagi, Haruna ^{[2
]}

Iizuka, Shunsuke ^{[2
]}

Ohtsuki, Kota ^{[2
]}

Imakiire, Atsushi ^{[2
]}

Nagashima, Takashi ^{[3
]}

Okamoto, Shinichiro ^{[4
,5
]}

Higuchi, Takashi ^{[1
]}

Shimada, Yohta ^{[1
]}

Hioki, Hiroyuki ^{[4
]}

Sonoda, Hiroyuki ^{[2
]}

Watabe, Ayako M. ^{[3
]}

Ohashi, Toya ^{[6
]}

Kobayashi, Hiroshi ^{[1
]}

机构：

[1] Jikei Univ, Div Gene Therapy, Res Ctr Med Sci, Sch Med, Tokyo, Japan

[2] JCR Pharmaceut Co Ltd, Kobe, Hyogo, Japan

[3] Jikei Univ, Inst Clin Med & Res, Res Ctr Med Sci, Sch Med, Chiba, Japan

[4] Juntendo Univ, Dept Neuroanat, Grad Sch Med, Tokyo, Japan

[5] Juntendo Univ, Adv Res Inst Hlth Sci, Tokyo, Japan

[6] Jikei Univ, Sch Nursing, Tokyo, Japan

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1344

引用

页码：635 / 636

页数：2

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